(en)E.M. Welch et al., « PTC124 targets genetic disorders caused by nonsense mutations », Nature, vol. 447, no 7140, , p. 87-91 (PMID17450125, lire en ligne [html], consulté le )modifier
(en)S. Hirawat et al., « Safety, tolerability, and pharmacokinetics of PTC124, a nonaminoglycoside nonsense mutation suppressor, following single- and multiple-dose administration to healthy male and female adult volunteers », Journal of clinical pharmacology, vol. 47, no 4, , p. 430-444 (PMID17389552, lire en ligne [html], consulté le )modifier
(en)E.M. Welch et al., « PTC124 targets genetic disorders caused by nonsense mutations », Nature, vol. 447, no 7140, , p. 87-91 (PMID17450125, lire en ligne [html], consulté le )modifier
(en)S. Hirawat et al., « Safety, tolerability, and pharmacokinetics of PTC124, a nonaminoglycoside nonsense mutation suppressor, following single- and multiple-dose administration to healthy male and female adult volunteers », Journal of clinical pharmacology, vol. 47, no 4, , p. 430-444 (PMID17389552, lire en ligne [html], consulté le )modifier