Draper, BW; Morcos, PA, Kimmel, CB (2001). «Inhibition of zebrafish fgf8 pre-mRNA splicing with morpholino oligos: A quantifiable method for gene knockdown.». Genesis (em inglês). 30 (3): 154–6. PMID11477696. doi:10.1002/gene.1053 !CS1 manut: Nomes múltiplos: lista de autores (link)
Heasman J (2002). «Morpholino oligos: making sense of antisense?». Dev. Biol. (em inglês). 243 (2): 209–14. PMID11884031. doi:10.1006/dbio.2001.0565
McClorey, G; Fall AM, Moulton HM, Iversen PL, Rasko JE, Ryan M, Fletcher S, Wilton SD (2006). «Induced dystrophin exon skipping in human muscle explants.». Neuromuscul Disord. (em inglês). 16 (9-10): 583–90. PMID16919955. doi:10.1016/j.nmd.2006.05.017 !CS1 manut: Nomes múltiplos: lista de autores (link)
Morcos, PA (2001). «Achieving efficient delivery of morpholino oligos in cultured cells.». Genesis (em inglês). 30 (3): 94–102. PMID11477682. doi:10.1002/gene.1039
Nasevicius, A; Ekker SC (2000). «Effective targeted gene 'knockdown' in zebrafish.». Nature Genetics (em inglês). 26 (2): 216–20. PMID11017081. doi:10.1038/79951
Heasman, J; Kofron M, Wylie C (2000). «Beta-catenin signaling activity dissected in the early Xenopus embryo: a novel antisense approach.». Developmental Biology (em inglês). 222 (1): 124–34. PMID10885751. doi:10.1006/dbio.2000.9720
Summerton, JE (2005). «Endo-porter: a novel reagent for safe, effective delivery of substances into cells.». Ann N Y Acad Sci. (em inglês). 1058: 62–75. PMID16394126. doi:10.1196/annals.1359.012
Coonrod, SA; Bolling LC, Wright PW, Visconti PE, Herr JC (2001). «A morpholino phenocopy of the mouse MOS mutation.». Genesis (em inglês). 30 (3): 198–200. PMID11477708. doi:10.1002/gene.1065 !CS1 manut: Nomes múltiplos: lista de autores (link)
Stancheva, I; Collins AL; Van den Veyver IB; Zoghbi H; Meehan RR (2003). «A mutant form of MeCP2 protein associated with human Rett syndrome cannot be displaced from methylated DNA by notch in Xenopus embryos». Mol Cell (em inglês). 12 (2): 425–35. PMID14536082. doi:10.1016/S1097-2765(03)00276-4 See Figure 1
Bruno, IG; Jin W; Cote GJ (2004). «Correction of aberrant FGFR1 alternative RNA splicing through targeting of intronic regulatory elements». Hum Mol Genet. 13 (20): 2409–20. PMID15333583. doi:10.1093/hmg/ddh272
Vetrini, F; Tammaro R; Bondanza S; Surace EM; Auricchio A; De Luca M; Ballabio A; Marigo V (2006). «Aberrant splicing in the ocular albinism type 1 gene (OA1/GPR143) is corrected in vitro by Morpholino antisense oligonucleotides». Hum Mutat. 27 (5): 420–6. PMID16550551. doi:10.1002/humu.20303
Morcos, PA (2007). «Achieving targeted and quantifiable alteration of mRNA splicing with Morpholino oligos». Biochem Biophys Res Commun. 358 (2): 521–7. PMID17493584. doi:10.1016/j.bbrc.2007.04.172
König, H; Matter N; Bader R; Thiele W; Müller F (2007). «Splicing Segregation: The Minor Spliceosome Acts outside the Nucleus and Controls Cell Proliferation». Cell. 131 (4): 718–29. PMID18022366. doi:10.1016/j.cell.2007.09.043
Yen, L; Svendsen J; Lee JS; Gray JT; Magnier M; Baba T; D'Amato RJ; Mulligan RC (2004). «Exogenous control of mammalian gene expression through modulation of RNA self-cleavage». Nature. 431 (7007): 471–6. PMID15386015. doi:10.1038/nature02844
Kamachi, Y; Okuda Y, Kondoh H (2008). «Quantitative Assessment of the Knockdown Efficiency of Morpholino Antisense Oligonucleotides in Zebrafish Embryos Using a Luciferase Assay». Genesis. 46 (1): 1–7. PMID18196596. doi:10.1002/dvg.20361
Morcos, PA; Li YF; Jiang S (2008). «Vivo-Morpholinos: A non-peptide transporter delivers Morpholinos into a wide array of mouse tissues». BioTechniques. 45 (6): 616–26. PMID19238792. doi:10.2144/000113005
Cerda, GA; Thomas JE; Allende ML; Karlstrom RO; Palma V (2006). «Electroporation of DNA, RNA, and Morpholinos into zebrafish embryos». Methods. 39 (3): 207–11. PMID16837210. doi:10.1016/j.ymeth.2005.12.009
Jubin, R (2004). «Optimizing electroporation conditions for intracellular delivery of Morpholino antisense oligonucleotides directed against the hepatitis C virus internal ribosome entry site». Methods Mol Med. 106: 309–22. PMID15375324. doi:10.1385/1-59259-854-4:309
Partridge, M; Vincent A; Matthews P; Puma J; Stein D; Summerton J (1996). «A simple method for delivering Morpholino antisense oligos into the cytoplasm of cells». Antisense Nucleic Acid Drug Dev. 6 (3): 169–75. PMID8915501. doi:10.1089/oli.1.1996.6.169
Fletcher, S; Honeyman K; Fall AM; Harding PL; Johnsen RD; Wilton SD (2006). «Dystrophin expression in the mdx mouse after localised and systemic administration of a Morpholino antisense oligonucleotide». J Gene Med. 8 (2): 207–16. PMID16285002. doi:10.1002/jgm.838
Kipshidze NN, Kim HS, Iversen P, Yazdi HA, Bhargava B, New G, Mehran R, Tio F, Haudenschild C, Dangas G, Stone GW, Iyer S, Roubin GS, Leon MB, Moses JW (2002). «Intramural coronary delivery of advanced antisense oligonucleotides reduces neointimal formation in the porcine stent restenosis model». J Am Coll Cardiol. 39 (10): 1686–91. PMID12020498. doi:10.1016/S0735-1097(02)01830-2
Abes, S; Moulton HM; Clair P; Prevot P; Youngblood DS; Wu RP; Iversen PL; Lebleu B (2006). «Vectorization of Morpholino oligomers by the (R-Ahx-R)(4) peptide allows efficient splicing correction in the absence of endosomolytic agents». J Control Release. 116 (3): 304–13. PMID17097177. doi:10.1016/j.jconrel.2006.09.011
Li, YF; Morcos PA (2008). «Design and Synthesis of Dendritic Molecular Transporter that Achieves Efficient in Vivo Delivery of Morpholino Antisense Oligo». Bioconjug Chem. 19 (7): 1464–70. PMID18564870. doi:10.1021/bc8001437
Summerton, J (1999). «Morpholino Antisense Oligomers: The Case for an RNase-H Independent Structural Type.». Biochimica et Biophysica Acta (em inglês). 1489 (1): 141–58. PMID10807004
Draper, BW; Morcos, PA, Kimmel, CB (2001). «Inhibition of zebrafish fgf8 pre-mRNA splicing with morpholino oligos: A quantifiable method for gene knockdown.». Genesis (em inglês). 30 (3): 154–6. PMID11477696. doi:10.1002/gene.1053 !CS1 manut: Nomes múltiplos: lista de autores (link)
Heasman J (2002). «Morpholino oligos: making sense of antisense?». Dev. Biol. (em inglês). 243 (2): 209–14. PMID11884031. doi:10.1006/dbio.2001.0565
McClorey, G; Fall AM, Moulton HM, Iversen PL, Rasko JE, Ryan M, Fletcher S, Wilton SD (2006). «Induced dystrophin exon skipping in human muscle explants.». Neuromuscul Disord. (em inglês). 16 (9-10): 583–90. PMID16919955. doi:10.1016/j.nmd.2006.05.017 !CS1 manut: Nomes múltiplos: lista de autores (link)
Summerton, J; Weller D (1997). «Morpholino Antisense Oligomers: Design, Preparation and Properties.». Antisense & Nucleic Acid Drug Development (em inglês). 7* (3): 187–95. PMID9212909
Morcos, PA (2001). «Achieving efficient delivery of morpholino oligos in cultured cells.». Genesis (em inglês). 30 (3): 94–102. PMID11477682. doi:10.1002/gene.1039
Nasevicius, A; Ekker SC (2000). «Effective targeted gene 'knockdown' in zebrafish.». Nature Genetics (em inglês). 26 (2): 216–20. PMID11017081. doi:10.1038/79951
Heasman, J; Kofron M, Wylie C (2000). «Beta-catenin signaling activity dissected in the early Xenopus embryo: a novel antisense approach.». Developmental Biology (em inglês). 222 (1): 124–34. PMID10885751. doi:10.1006/dbio.2000.9720
Howard, EW; Newman LA, Oleksyn DW, Angerer RC, Angerer LM (2001). «SpKrl: a direct target of (beta)-catenin regulation required for endoderm differentiation in sea urchin embryos.». Development (em inglês). 128 (3): 365–75. PMID11152635 !CS1 manut: Nomes múltiplos: lista de autores (link)
Kos, R; Reedy MV, Johnson RL, Erickson CA (2001). «The winged-helix transcription factor FoxD3 is important for establishing the neural crest lineage and repressing melanogenesis in avian embryos.». Development (em inglês). 128 (8): 1467–79. PMID11262245 !CS1 manut: Nomes múltiplos: lista de autores (link)
Summerton, JE (2005). «Endo-porter: a novel reagent for safe, effective delivery of substances into cells.». Ann N Y Acad Sci. (em inglês). 1058: 62–75. PMID16394126. doi:10.1196/annals.1359.012
Coonrod, SA; Bolling LC, Wright PW, Visconti PE, Herr JC (2001). «A morpholino phenocopy of the mouse MOS mutation.». Genesis (em inglês). 30 (3): 198–200. PMID11477708. doi:10.1002/gene.1065 !CS1 manut: Nomes múltiplos: lista de autores (link)
Stancheva, I; Collins AL; Van den Veyver IB; Zoghbi H; Meehan RR (2003). «A mutant form of MeCP2 protein associated with human Rett syndrome cannot be displaced from methylated DNA by notch in Xenopus embryos». Mol Cell (em inglês). 12 (2): 425–35. PMID14536082. doi:10.1016/S1097-2765(03)00276-4 See Figure 1
Bruno, IG; Jin W; Cote GJ (2004). «Correction of aberrant FGFR1 alternative RNA splicing through targeting of intronic regulatory elements». Hum Mol Genet. 13 (20): 2409–20. PMID15333583. doi:10.1093/hmg/ddh272
Vetrini, F; Tammaro R; Bondanza S; Surace EM; Auricchio A; De Luca M; Ballabio A; Marigo V (2006). «Aberrant splicing in the ocular albinism type 1 gene (OA1/GPR143) is corrected in vitro by Morpholino antisense oligonucleotides». Hum Mutat. 27 (5): 420–6. PMID16550551. doi:10.1002/humu.20303
Morcos, PA (2007). «Achieving targeted and quantifiable alteration of mRNA splicing with Morpholino oligos». Biochem Biophys Res Commun. 358 (2): 521–7. PMID17493584. doi:10.1016/j.bbrc.2007.04.172
König, H; Matter N; Bader R; Thiele W; Müller F (2007). «Splicing Segregation: The Minor Spliceosome Acts outside the Nucleus and Controls Cell Proliferation». Cell. 131 (4): 718–29. PMID18022366. doi:10.1016/j.cell.2007.09.043
Yen, L; Svendsen J; Lee JS; Gray JT; Magnier M; Baba T; D'Amato RJ; Mulligan RC (2004). «Exogenous control of mammalian gene expression through modulation of RNA self-cleavage». Nature. 431 (7007): 471–6. PMID15386015. doi:10.1038/nature02844
Kamachi, Y; Okuda Y, Kondoh H (2008). «Quantitative Assessment of the Knockdown Efficiency of Morpholino Antisense Oligonucleotides in Zebrafish Embryos Using a Luciferase Assay». Genesis. 46 (1): 1–7. PMID18196596. doi:10.1002/dvg.20361
Morcos, PA; Li YF; Jiang S (2008). «Vivo-Morpholinos: A non-peptide transporter delivers Morpholinos into a wide array of mouse tissues». BioTechniques. 45 (6): 616–26. PMID19238792. doi:10.2144/000113005
Cerda, GA; Thomas JE; Allende ML; Karlstrom RO; Palma V (2006). «Electroporation of DNA, RNA, and Morpholinos into zebrafish embryos». Methods. 39 (3): 207–11. PMID16837210. doi:10.1016/j.ymeth.2005.12.009
Jubin, R (2004). «Optimizing electroporation conditions for intracellular delivery of Morpholino antisense oligonucleotides directed against the hepatitis C virus internal ribosome entry site». Methods Mol Med. 106: 309–22. PMID15375324. doi:10.1385/1-59259-854-4:309
Partridge, M; Vincent A; Matthews P; Puma J; Stein D; Summerton J (1996). «A simple method for delivering Morpholino antisense oligos into the cytoplasm of cells». Antisense Nucleic Acid Drug Dev. 6 (3): 169–75. PMID8915501. doi:10.1089/oli.1.1996.6.169
Fletcher, S; Honeyman K; Fall AM; Harding PL; Johnsen RD; Wilton SD (2006). «Dystrophin expression in the mdx mouse after localised and systemic administration of a Morpholino antisense oligonucleotide». J Gene Med. 8 (2): 207–16. PMID16285002. doi:10.1002/jgm.838
Kipshidze NN, Kim HS, Iversen P, Yazdi HA, Bhargava B, New G, Mehran R, Tio F, Haudenschild C, Dangas G, Stone GW, Iyer S, Roubin GS, Leon MB, Moses JW (2002). «Intramural coronary delivery of advanced antisense oligonucleotides reduces neointimal formation in the porcine stent restenosis model». J Am Coll Cardiol. 39 (10): 1686–91. PMID12020498. doi:10.1016/S0735-1097(02)01830-2
Abes, S; Moulton HM; Clair P; Prevot P; Youngblood DS; Wu RP; Iversen PL; Lebleu B (2006). «Vectorization of Morpholino oligomers by the (R-Ahx-R)(4) peptide allows efficient splicing correction in the absence of endosomolytic agents». J Control Release. 116 (3): 304–13. PMID17097177. doi:10.1016/j.jconrel.2006.09.011
Li, YF; Morcos PA (2008). «Design and Synthesis of Dendritic Molecular Transporter that Achieves Efficient in Vivo Delivery of Morpholino Antisense Oligo». Bioconjug Chem. 19 (7): 1464–70. PMID18564870. doi:10.1021/bc8001437