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Charles J. Parker, Mitsuhiro Omine, Stephen Richards, Jun-ichi Nishimura, Monica Bessler, Russell Ware, Peter Hillmen, Lucio Luzzatto, Neal S. Young, Taroh Kinoshita, Wendell Rosse, Gerard Socié: Diagnosis and management of paroxysmal nocturnal hemoglobinuria. In: Blood. Band106, Nr.12, 1. Dezember 2005, ISSN0006-4971, S.3699–3709, doi:10.1182/blood-2005-04-1717, PMID 16051736, PMC 1895106 (freier Volltext) – (bloodjournal.org [abgerufen am 24. Juli 2020]).
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Thomas Hale Ham, John H. Dingle: Studies on Destruction of Red Blood Cells. II. Chronic Hemolytic Anemia With Paroxysmal Nocturnal Hemoglobinuria: Certain Immunological Aspects of the Hemolytic Mechanism With Special Reference to Serum Complement 1. In: Journal of Clinical Investigation. Band18, Nr.6, 1. November 1939, ISSN0021-9738, S.657–672, doi:10.1172/JCI101081, PMID 16694699, PMC 434913 (freier Volltext).
M. Takahashi, J. Takeda, S. Hirose, R. Hyman, N. Inoue: Deficient biosynthesis of N-acetylglucosaminyl-phosphatidylinositol, the first intermediate of glycosyl phosphatidylinositol anchor biosynthesis, in cell lines established from patients with paroxysmal nocturnal hemoglobinuria. In: Journal of Experimental Medicine. Band177, Nr.2, 1. Februar 1993, ISSN0022-1007, S.517–521, doi:10.1084/jem.177.2.517, PMID 8426120, PMC 2190897 (freier Volltext) – (rupress.org [abgerufen am 29. März 2020]).
Junji Takeda, Toshio Miyata, Kazuyoshi Kawagoe, Yoshiyasu Iida, Yuichi Endo: Deficiency of the GPI anchor caused by a somatic mutation of the PIG-A gene in paroxysmal nocturnal hemoglobinuria. In: Cell. Band73, Nr.4, 21. Mai 1993, ISSN0092-8674, S.703–711, doi:10.1016/0092-8674(93)90250-T, PMID 8500164.
onkopedia.com
Jörg Schubert, Alexander Röth, Peter Bettelheim, Georg Stüssi, Britta Höchsmann, Jens Panse, Tim Henrik Brümmendorf, Hubert Schrezenmeier: Paroxysmale nächtliche Hämoglobinurie (PNH). DGHO-Leitlinie auf onkopedia.com, Stand November 2019. Zuletzt abgerufen am 20. März 2020.
roche.com
Pipeline, Website Roche, abgerufen am 8. Februar 2023
rupress.org
M. Takahashi, J. Takeda, S. Hirose, R. Hyman, N. Inoue: Deficient biosynthesis of N-acetylglucosaminyl-phosphatidylinositol, the first intermediate of glycosyl phosphatidylinositol anchor biosynthesis, in cell lines established from patients with paroxysmal nocturnal hemoglobinuria. In: Journal of Experimental Medicine. Band177, Nr.2, 1. Februar 1993, ISSN0022-1007, S.517–521, doi:10.1084/jem.177.2.517, PMID 8426120, PMC 2190897 (freier Volltext) – (rupress.org [abgerufen am 29. März 2020]).
sciencedirect.com
Thomas C. Thomas, Scott A. Rollins, Russell P. Rother, Michelle A. Giannoni, Sandra L. Hartman: Inhibition of complement activity by humanized anti-C5 antibody and single-chain Fv. In: Molecular Immunology. Band33, Nr.17, 1. Dezember 1996, ISSN0161-5890, S.1389–1401, doi:10.1016/S0161-5890(96)00078-8 (sciencedirect.com [abgerufen am 29. März 2020]).
zdb-katalog.de
Gerard Socié, Hubert Schrezenmeier, Petra Muus, I. Lisukov, Alexander Röth: Changing prognosis in paroxysmal nocturnal haemoglobinuria disease subcategories: an analysis of the International PNH Registry. In: Internal Medicine Journal. Band46, Nr.9, 2016, ISSN1445-5994, S.1044–1053, doi:10.1111/imj.13160.
Anita Hill, Amy E. DeZern, Taroh Kinoshita, Robert A. Brodsky: Paroxysmal nocturnal haemoglobinuria. In: Nature Reviews Disease Primers. Band3, Nr.1, 18. Mai 2017, ISSN2056-676X, S.1–14, doi:10.1038/nrdp.2017.28.
Charles J. Parker: Historical aspects of paroxysmal nocturnal haemoglobinuria: 'defining the disease'. In: British Journal of Haematology. Band117, Nr.1, April 2002, ISSN0007-1048, S.3–22, doi:10.1046/j.1365-2141.2002.03374.x.
Charles J. Parker, Mitsuhiro Omine, Stephen Richards, Jun-ichi Nishimura, Monica Bessler, Russell Ware, Peter Hillmen, Lucio Luzzatto, Neal S. Young, Taroh Kinoshita, Wendell Rosse, Gerard Socié: Diagnosis and management of paroxysmal nocturnal hemoglobinuria. In: Blood. Band106, Nr.12, 1. Dezember 2005, ISSN0006-4971, S.3699–3709, doi:10.1182/blood-2005-04-1717, PMID 16051736, PMC 1895106 (freier Volltext) – (bloodjournal.org [abgerufen am 24. Juli 2020]).
Thomas C. Thomas, Scott A. Rollins, Russell P. Rother, Michelle A. Giannoni, Sandra L. Hartman: Inhibition of complement activity by humanized anti-C5 antibody and single-chain Fv. In: Molecular Immunology. Band33, Nr.17, 1. Dezember 1996, ISSN0161-5890, S.1389–1401, doi:10.1016/S0161-5890(96)00078-8 (sciencedirect.com [abgerufen am 29. März 2020]).
John Marks: THE MARCHIAFAVA MICHELI SYNDROME (Paroxysmal Nocturnal Haemoglobinuria). In: QJM: An International Journal of Medicine. Band18, Nr.2, 1. April 1949, ISSN1460-2725, S.105–121, doi:10.1093/oxfordjournals.qjmed.a066527.
Thomas Hale Ham, John H. Dingle: Studies on Destruction of Red Blood Cells. II. Chronic Hemolytic Anemia With Paroxysmal Nocturnal Hemoglobinuria: Certain Immunological Aspects of the Hemolytic Mechanism With Special Reference to Serum Complement 1. In: Journal of Clinical Investigation. Band18, Nr.6, 1. November 1939, ISSN0021-9738, S.657–672, doi:10.1172/JCI101081, PMID 16694699, PMC 434913 (freier Volltext).
M. Takahashi, J. Takeda, S. Hirose, R. Hyman, N. Inoue: Deficient biosynthesis of N-acetylglucosaminyl-phosphatidylinositol, the first intermediate of glycosyl phosphatidylinositol anchor biosynthesis, in cell lines established from patients with paroxysmal nocturnal hemoglobinuria. In: Journal of Experimental Medicine. Band177, Nr.2, 1. Februar 1993, ISSN0022-1007, S.517–521, doi:10.1084/jem.177.2.517, PMID 8426120, PMC 2190897 (freier Volltext) – (rupress.org [abgerufen am 29. März 2020]).
Toshio Miyata, Junji Takeda, Yoshiyasu Iida, Norio Yamada, Norimitsu Inoue, Minoru Takahashi, Kenji Maeda, Teruo Kitani, Taroh Kinoshita: The cloning of PIG-A, a component in the early step of GPI-anchor biosynthesis. In: Science. Band259, Nr.5099, 26. Februar 1993, ISSN0036-8075, S.1318–1320, doi:10.1126/science.7680492.
Junji Takeda, Toshio Miyata, Kazuyoshi Kawagoe, Yoshiyasu Iida, Yuichi Endo: Deficiency of the GPI anchor caused by a somatic mutation of the PIG-A gene in paroxysmal nocturnal hemoglobinuria. In: Cell. Band73, Nr.4, 21. Mai 1993, ISSN0092-8674, S.703–711, doi:10.1016/0092-8674(93)90250-T, PMID 8500164.
