Gene therapy (English Wikipedia)
Analysis of information sources in references of the Wikipedia article "Gene therapy" in English language version.
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aabb.org (Global: low place; English: low place)
- "FDA Approves First T-Cell Receptor Gene Therapy For Solid Tumors". AABB News & Resources. 6 August 2024. Retrieved 19 September 2024.[dead link]
abedia.com (Global: low place; English: low place)
- "Gene Therapy Clinical Trials Worldwide Database". The Journal of Gene Medicine. Wiley. June 2016. Archived from the original on 31 July 2020.
adsabs.harvard.edu (Global: 14th place; English: 9th place)
ui.adsabs.harvard.edu
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- Gupta RM, Musunuru K (October 2014). "Expanding the genetic editing tool kit: ZFNs, TALENs, and CRISPR-Cas9". The Journal of Clinical Investigation. 124 (10): 4154–61. Bibcode:2014JCliI.124.4154G. doi:10.1172/JCI72992. PMC 4191047. PMID 25271723.
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- Friedmann T, Roblin R (March 1972). "Gene therapy for human genetic disease?". Science. 175 (4025): 949–955. Bibcode:1972Sci...175..949F. doi:10.1126/science.175.4025.949. PMID 5061866. S2CID 19952096.
- Blaese RM, Culver KW, Miller AD, Carter CS, Fleisher T, Clerici M, et al. (October 1995). "T lymphocyte-directed gene therapy for ADA- SCID: initial trial results after 4 years". Science. 270 (5235): 475–480. Bibcode:1995Sci...270..475B. doi:10.1126/science.270.5235.475. PMID 7570001. S2CID 46339645.
- Trojan J, Johnson TR, Rudin SD, Ilan J, Tykocinski ML, Ilan J (January 1993). "Treatment and prevention of rat glioblastoma by immunogenic C6 cells expressing antisense insulin-like growth factor I RNA". Science. 259 (5091): 94–97. Bibcode:1993Sci...259...94T. doi:10.1126/science.8418502. PMID 8418502.
- Abbott A (April 1992). "Gene therapy. Italians first to use stem cells". Nature. 356 (6369): 465. Bibcode:1992Natur.356..465A. doi:10.1038/356465a0. PMID 1560817. S2CID 4319842.
- Cavazzana-Calvo M, Thrasher A, Mavilio F (February 2004). "The future of gene therapy". Nature. 427 (6977): 779–781. Bibcode:2004Natur.427..779C. doi:10.1038/427779a. hdl:11380/307566. PMID 14985734. S2CID 4421364.
- Naldini, Luigi; Blömer, Ulrike; Gallay, Philippe; Ory, Daniel; Mulligan, Richard; Gage, Fred H.; Verma, Inder M.; Trono, Didier (12 April 1996). "In Vivo Gene Delivery and Stable Transduction of Nondividing Cells by a Lentiviral Vector". Science. 272 (5259): 263–267. Bibcode:1996Sci...272..263N. doi:10.1126/science.272.5259.263. ISSN 0036-8075. PMID 8602510. S2CID 18997464.
- Morgan RA, Dudley ME, Wunderlich JR, Hughes MS, Yang JC, Sherry RM, et al. (October 2006). "Cancer regression in patients after transfer of genetically engineered lymphocytes". Science. 314 (5796): 126–129. Bibcode:2006Sci...314..126M. doi:10.1126/science.1129003. PMC 2267026. PMID 16946036.
- Levine BL, Humeau LM, Boyer J, MacGregor RR, Rebello T, Lu X, et al. (November 2006). "Gene transfer in humans using a conditionally replicating lentiviral vector". Proceedings of the National Academy of Sciences of the United States of America. 103 (46): 17372–17377. Bibcode:2006PNAS..10317372L. doi:10.1073/pnas.0608138103. PMC 1635018. PMID 17090675.
- Cartier N, Hacein-Bey-Abina S, Bartholomae CC, Veres G, Schmidt M, Kutschera I, et al. (November 2009). "Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy" (PDF). Science. 326 (5954): 818–823. Bibcode:2009Sci...326..818C. doi:10.1126/science.1171242. PMID 19892975. S2CID 27783.
- Cavazzana-Calvo M, Payen E, Negre O, Wang G, Hehir K, Fusil F, et al. (September 2010). "Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia". Nature. 467 (7313): 318–322. Bibcode:2010Natur.467..318C. doi:10.1038/nature09328. PMC 3355472. PMID 20844535.
- Gardner MR, Kattenhorn LM, Kondur HR, von Schaewen M, Dorfman T, Chiang JJ, et al. (March 2015). "AAV-expressed eCD4-Ig provides durable protection from multiple SHIV challenges". Nature. 519 (7541): 87–91. Bibcode:2015Natur.519...87G. doi:10.1038/nature14264. PMC 4352131. PMID 25707797.
- Cyranoski D (July 2016). "Chinese scientists to pioneer first human CRISPR trial". Nature. 535 (7613): 476–477. Bibcode:2016Natur.535..476C. doi:10.1038/nature.2016.20302. PMID 27466105.
- Ledford H (March 2020). "CRISPR treatment inserted directly into the body for first time". Nature. 579 (7798): 185. Bibcode:2020Natur.579..185L. doi:10.1038/d41586-020-00655-8. PMID 32157225.
- Pearson TS, Gupta N, San Sebastian W, Imamura-Ching J, Viehoever A, Grijalvo-Perez A, et al. (July 2021). "Gene therapy for aromatic L-amino acid decarboxylase deficiency by MR-guided direct delivery of AAV2-AADC to midbrain dopaminergic neurons". Nature Communications. 12 (1) 4251. Bibcode:2021NatCo..12.4251P. doi:10.1038/s41467-021-24524-8. PMC 8275582. PMID 34253733.
aetion.com (Global: low place; English: low place)
- "EMA-approved application for Zolgensma". Aetion (Press release). Archived from the original on 23 July 2021. Retrieved 23 July 2021.
allfordrugs.com (Global: low place; English: low place)
- Crasto AM (7 July 2013). "Glybera – The Most Expensive Drug in the world & First Approved Gene Therapy in the West". All About Drugs. Retrieved 2 November 2013.
ama-assn.org (Global: 4,430th place; English: 4,511th place)
- "Gene Therapy". ama-assn.org. 4 April 2014. Archived from the original on 15 March 2015. Retrieved 22 March 2015.
apnews.com (Global: 101st place; English: 62nd place)
- "Tests suggest scientists achieved 1st 'in body' gene editing". AP NEWS. 7 February 2019. Retrieved 17 November 2020.
- "AP Exclusive: US scientists try 1st gene editing in the body". AP NEWS. 15 November 2017. Retrieved 17 November 2020.
- Marchione M (7 February 2019). "Tests suggest scientists achieved 1st 'in body' gene editing". AP News. Retrieved 7 February 2019.
- "Gene therapy eyedrops restored a boy's sight. Similar treatments could help millions". AP News. 24 July 2023. Retrieved 31 July 2023.
archive.org (Global: 6th place; English: 6th place)
- Strachnan T, Read AP (2004). Human Molecular Genetics (3rd ed.). Garland Publishing. p. 616. ISBN 978-0-8153-4184-0.
archives-ouvertes.fr (Global: 1,143rd place; English: 973rd place)
hal-cea.archives-ouvertes.fr
- Cartier N, Hacein-Bey-Abina S, Bartholomae CC, Veres G, Schmidt M, Kutschera I, et al. (November 2009). "Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy" (PDF). Science. 326 (5954): 818–823. Bibcode:2009Sci...326..818C. doi:10.1126/science.1171242. PMID 19892975. S2CID 27783.
arhp.org (Global: low place; English: low place)
- "Human Cloning and Genetic Modification". Association of Reproductive Health Officials. 2013. Archived from the original on 18 June 2013.
arxiv.org (Global: 49th place; English: 31st place)
- https://arxiv.org/pdf/2603.19473 Gene therapy foundations
asgct.org (Global: low place; English: low place)
- "Gene & Cell Therapy FAQs | ASGCT - American Society of Gene & Cell Therapy | ASGCT - American Society of Gene & Cell Therapy". asgct.org. Archived from the original on 23 July 2021. Retrieved 23 July 2021.
audentestx.com (Global: low place; English: low place)
- "Audentes Therapeutics Provides Update on the ASPIRO Clinical Trial Evaluating AT132 in Patients with X-linked Myotubular Myopathy". Audentes Therapeutics. 10 August 2020. Archived from the original on 27 October 2020. Retrieved 21 September 2020.
bbc.co.uk (Global: 11th place; English: 10th place)
bbc.co.uk
- Ghosh P (28 April 2016). "Gene therapy reverses sight loss and is long-lasting". BBC News Online. Retrieved 29 April 2016.
- Gallagher J (2 November 2012). "Gene therapy: Glybera approved by European Commission". BBC News. Retrieved 15 December 2012.
- Gallagher J (21 April 2015). "Gene therapy: 'Tame HIV' used to cure disease". BBC News, Health. Retrieved 21 April 2015.
- Walsh F (3 December 2015). "Gene editing: Is era of designer humans getting closer?". BBC News Health. Retrieved 31 December 2015.
- "Base editing: Revolutionary therapy clears girl's incurable cancer". BBC News. 11 December 2022. Retrieved 11 December 2022.
news.bbc.co.uk
- "Gene therapy first for poor sight". BBC News. 1 May 2007. Retrieved 3 May 2010.
bbc.com (Global: 26th place; English: 23rd place)
- "'Designer cells' reverse one-year-old's cancer". BBC News. 5 November 2015. Retrieved 11 December 2022.
- "HIV used to cure 'bubble boy' disease". BBC News. 17 April 2019. Retrieved 19 July 2021.
- "Transformational therapy cures haemophilia B". BBC News. 21 July 2022. Retrieved 3 August 2022.
bionews.org.uk (Global: low place; English: low place)
- "Gene therapy approved in Europe for first time". Archived from the original on 4 January 2014.
- Reeves R (6 June 2016). "Second gene therapy wins approval in Europe". Bionews. Archived from the original on 21 February 2017. Retrieved 20 February 2017.
books.google.com (Global: 3rd place; English: 3rd place)
- U.S. Congress, Office of Technology Assessment (December 1984). Human gene therapy – A background paper. DIANE Publishing. ISBN 978-1-4289-2371-3.
- Lowenstein PR (2008). "Gene Therapy for Neurological Disorders: New Therapies or Human Experimentation?". In Burley J, Harris J (eds.). A Companion to Genethics. John Wiley & Sons. ISBN 978-0-470-75637-9.
bostonglobe.com (Global: 657th place; English: 344th place)
- "Ten things you might have missed Monday from the world of business". Boston Globe. 3 February 2015. Retrieved 13 February 2015.
cancer.gov (Global: 1,906th place; English: 1,649th place)
- "FDA Approves T-VEC to Treat Metastatic Melanoma". National Cancer Institute. 25 November 2015. Retrieved 23 July 2021.
celladon.com (Global: low place; English: low place)
ir.celladon.com
- "Celladon Receives Breakthrough Therapy Designation From FDA for Mydicar, Novel, First-in-Class Therapy in Development to Treat Heart Failure". Celladon. 10 July 2015. Archived from the original on 10 July 2015. Retrieved 2 January 2022.
cioms.ch (Global: low place; English: low place)
- "The Declaration of Inuyama: Human Genome Mapping, Genetic Screening and Gene Therapy". Council for International Organizations of Medical Sciences. Archived from the original on 5 August 2001.
clinicaltrials.gov (Global: 4,259th place; English: 3,081st place)
- Clinical trial number NCT01639690 for "β-Thalassemia Major With Autologous CD34+ Hematopoietic Progenitor Cells Transduced With TNS9.3.55 a Lentiviral Vector Encoding the Normal Human β-Globin Gene" at ClinicalTrials.gov
- Clinical trial number NCT02247843 for "Stem Cell Gene Therapy for Sickle Cell Disease" at ClinicalTrials.gov
- Clinical trial number NCT00012545 for "Collection and Storage of Umbilical Cord Stem Cells for Treatment of Sickle Cell Disease" at ClinicalTrials.gov
- Staff (2 February 2019). "Ascending Dose Study of Genome Editing by the Zinc Finger Nuclease (ZFN) Therapeutic SB-913 in Subjects With MPS II". ClinicalTrials.gov. U.S. National Library of Medicine. Retrieved 7 February 2019.
- "Single Ascending Dose Study in Participants With LCA10". clinicaltrials.gov. Retrieved 20 August 2019.
crisprmedicinenews.com (Global: low place; English: low place)
- "News: Clinical Trial Update: Positive Data for First Ever In Vivo CRISPR Medicine". CRISPR Medicine. Retrieved 16 December 2021.
dddmag.com (Global: low place; English: low place)
- "Gene Therapy for PAD Approved". 6 December 2011. Retrieved 5 August 2015.
doi.org (Global: 2nd place; English: 2nd place)
- Kaji EH, Leiden JM (February 2001). "Gene and stem cell therapies". JAMA. 285 (5): 545–550. doi:10.1001/jama.285.5.545. PMID 11176856.
- Rosenberg SA, Aebersold P, Cornetta K, Kasid A, Morgan RA, Moen R, et al. (August 1990). "Gene transfer into humans--immunotherapy of patients with advanced melanoma, using tumor-infiltrating lymphocytes modified by retroviral gene transduction". The New England Journal of Medicine. 323 (9): 570–578. doi:10.1056/NEJM199008303230904. PMID 2381442.
- Gorell E, Nguyen N, Lane A, Siprashvili Z (April 2014). "Gene therapy for skin diseases". Cold Spring Harbor Perspectives in Medicine. 4 (4) a015149. doi:10.1101/cshperspect.a015149. PMC 3968787. PMID 24692191.
- Sun M (October 1982). "Martin Cline loses appeal on NIH grant". Science. 218 (4567): 37. Bibcode:1982Sci...218...37S. doi:10.1126/science.7123214. PMID 7123214.
- Sheridan C (February 2011). "Gene therapy finds its niche". Nature Biotechnology. 29 (2): 121–128. doi:10.1038/nbt.1769. PMID 21301435. S2CID 5063701.
- O'Malley BW, Ledley FD (October 1993). "Somatic gene therapy. Methods for the present and future". Arch Otolaryngol Head Neck Surg. 119 (10): 1100–7. doi:10.1001/archotol.1993.01880220044007. PMID 8398061.
- Oldfield EH, Ram Z, Culver KW, Blaese RM, DeVroom HL, Anderson WF (February 1993). "Gene therapy for the treatment of brain tumors using intra-tumoral transduction with the thymidine kinase gene and intravenous ganciclovir". Human Gene Therapy. 4 (1): 39–69. doi:10.1089/hum.1993.4.1-39. PMID 8384892.
- Maguire AM, Simonelli F, Pierce EA, Pugh EN, Mingozzi F, Bennicelli J, et al. (May 2008). "Safety and efficacy of gene transfer for Leber's congenital amaurosis". The New England Journal of Medicine. 358 (21): 2240–2248. doi:10.1056/NEJMoa0802315. PMC 2829748. PMID 18441370.
- Simonelli F, Maguire AM, Testa F, Pierce EA, Mingozzi F, Bennicelli JL, et al. (March 2010). "Gene therapy for Leber's congenital amaurosis is safe and effective through 1.5 years after vector administration". Molecular Therapy. 18 (3): 643–650. doi:10.1038/mt.2009.277. PMC 2839440. PMID 19953081.
- Cideciyan AV, Hauswirth WW, Aleman TS, Kaushal S, Schwartz SB, Boye SL, Windsor EA, Conlon TJ, Sumaroka A, Roman AJ, Byrne BJ, Jacobson SG (August 2009). "Vision 1 year after gene therapy for Leber's congenital amaurosis". The New England Journal of Medicine. 361 (7): 725–727. doi:10.1056/NEJMc0903652. PMC 2847775. PMID 19675341.
- Bainbridge JW, Smith AJ, Barker SS, Robbie S, Henderson R, Balaggan K, et al. (May 2008). "Effect of gene therapy on visual function in Leber's congenital amaurosis". The New England Journal of Medicine. 358 (21): 2231–2239. doi:10.1056/NEJMoa0802268. hdl:10261/271174. PMID 18441371.
- Fischer A, Hacein-Bey-Abina S, Cavazzana-Calvo M (June 2010). "20 years of gene therapy for SCID". Nature Immunology. 11 (6): 457–460. doi:10.1038/ni0610-457. PMID 20485269. S2CID 11300348.
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- Cartier N, Aubourg P (July 2010). "Hematopoietic stem cell transplantation and hematopoietic stem cell gene therapy in X-linked adrenoleukodystrophy". Brain Pathology. 20 (4): 857–862. doi:10.1111/j.1750-3639.2010.00394.x. PMC 8094635. PMID 20626747. S2CID 24182017.
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- Sherkow JS, Zettler PJ, Greely HT (December 2018). "Is it 'gene therapy'?". Journal of Law and the Biosciences. 5 (3): 786–793. doi:10.1093/jlb/lsy020. PMC 6534757. PMID 31143463.
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- Williams DA, Orkin SH (April 1986). "Somatic gene therapy. Current status and future prospects". The Journal of Clinical Investigation. 77 (4): 1053–6. doi:10.1172/JCI112403. PMC 424438. PMID 3514670.
- Mavilio F, Ferrari G (July 2008). "Genetic modification of somatic stem cells. The progress, problems and prospects of a new therapeutic technology". EMBO Reports. 9 (Suppl 1): S64–69. doi:10.1038/embor.2008.81. PMC 3327547. PMID 18578029.
- Mullard A (June 2020). "Gene-editing pipeline takes off". Nature Reviews. Drug Discovery. 19 (6): 367–372. doi:10.1038/d41573-020-00096-y. PMID 32415249. S2CID 218657910.
- MacLaren RE, Groppe M, Barnard AR, Cottriall CL, Tolmachova T, Seymour L, Clark KR, During MJ, Cremers FP, Black GC, Lotery AJ, Downes SM, Webster AR, Seabra MC (March 2014). "Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial". Lancet. 383 (9923): 1129–1137. doi:10.1016/S0140-6736(13)62117-0. PMC 4171740. PMID 24439297.
- Dever DP, Bak RO, Reinisch A, Camarena J, Washington G, Nicolas CE, et al. (November 2016). "CRISPR/Cas9 β-globin gene targeting in human haematopoietic stem cells". Nature. 539 (7629): 384–389. Bibcode:2016Natur.539..384D. doi:10.1038/nature20134. PMC 5898607. PMID 27820943.
- Gupta RM, Musunuru K (October 2014). "Expanding the genetic editing tool kit: ZFNs, TALENs, and CRISPR-Cas9". The Journal of Clinical Investigation. 124 (10): 4154–61. Bibcode:2014JCliI.124.4154G. doi:10.1172/JCI72992. PMC 4191047. PMID 25271723.
- Sanches-da-Silva GN, Medeiros LF, Lima FM (21 August 2019). "The Potential Use of the CRISPR-Cas System for HIV-1 Gene Therapy". International Journal of Genomics. 2019 8458263. doi:10.1155/2019/8458263. PMC 6721108. PMID 31531340.
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