Therapeutic gene modulation (English Wikipedia)

Analysis of information sources in references of the Wikipedia article "Therapeutic gene modulation" in English language version.

refsWebsite

Global rank English rank

53nih.gov

4^th place

34doi.org

2^nd place

10harvard.edu

18^th place

17^th place

5semanticscholar.org

11^th place

8^th place

2caltech.edu

887^th place

714^th place

1csic.es

2,323^rd place

3,364^th place

1handle.net

102^nd place

76^th place

1psu.edu

207^th place

136^th place

1clinicaltrials.gov

5,225^th place

4,062^nd place

caltech.edu

authors.library.caltech.edu

White S, Szewcxyk JW, Turner JM, Baird EE, Dervan PB (1998). "Recognition of the four Watson-Crick base pairs in the DNA minor groove by synthetic ligands" (PDF). Nature. 391 (6666): 468–471. Bibcode:1998Natur.391..468W. doi:10.1038/35106. PMID 9461213. S2CID 205023593.
Weyermann P, Dervan PB (2002). "Recognition of ten base pairs of DNA by head-to-head hairpin dimers" (PDF). J. Am. Chem. Soc. 124 (24): 6872–6878. doi:10.1021/ja020258k. PMID 12059208.

clinicaltrials.gov

"Identifier NCT00080392.Modulation of Vascular Endothelial Growth Factor (VEGF) Using an Engineered Zinc-Finger Transcription Factor to Treat Lower Limb Intermittent Claudication". ClinicalTrials.gov. U.S. National Institutes of Health. 30 December 2011. Retrieved 25 July 2013.

csic.es

digital.csic.es

Choo, Y.; Sánchez-García, I.; Klug, A. (December 1994). "In vivo repression by a site-specific DNA-binding protein designed against an oncogenic sequence" (PDF). Nature. 372 (6507): 642–5. Bibcode:1994Natur.372..642C. doi:10.1038/372642a0. hdl:10261/6295. PMID 7990954. S2CID 12701336.

doi.org

Young WB, Link CJ (2000). "Chimeric retroviral helper virus and picornavirus IRES sequence to eliminate DNA methylation for improved retroviral packaging cells". Journal of Virology. 74 (11): 5242–5249. doi:10.1128/JVI.74.11.5242-5249.2000. PMC 110878. PMID 10799600.
Uil TG, Haisma HJ, Rots MG (2003). "Therapeutic modulation of endogenous gene function by agents with designed DNA-sequence specificities". Nucleic Acids Research. 31 (21): 6064–6078. doi:10.1093/nar/gkg815. PMC 275457. PMID 14576293.
Sargent, RG.; Kim, S.; Gruenert, DC. (2011). "Oligo/polynucleotide-based gene modification: strategies and therapeutic potential". Oligonucleotides. 21 (2): 55–75. doi:10.1089/oli.2010.0273. PMC 3078494. PMID 21417933.
Simon, P.; Cannata, F.; Concordet, JP.; Giovannangeli, C. (August 2008). "Targeting DNA with triplex-forming oligonucleotides to modify gene sequence". Biochimie. 90 (8): 1109–16. doi:10.1016/j.biochi.2008.04.004. PMID 18460344.
Zhou, Y.; Kierzek, E.; Loo, ZP.; Antonio, M.; Yau, YH.; Chuah, YW.; Geifman-Shochat, S.; Kierzek, R.; Chen, G. (July 2013). "Recognition of RNA duplexes by chemically modified triplex-forming oligonucleotides". Nucleic Acids Res. 41 (13): 6664–73. doi:10.1093/nar/gkt352. PMC 3711454. PMID 23658228.
Guntaka, RV.; Varma, BR.; Weber, KT. (January 2003). "Triplex-forming oligonucleotides as modulators of gene expression". Int J Biochem Cell Biol. 35 (1): 22–31. doi:10.1016/s1357-2725(02)00165-6. PMID 12467644.
Faria, M.; Wood, CD.; Perrouault, L.; Nelson, JS.; Winter, A.; White, MR.; Helene, C.; Giovannangeli, C. (April 2000). "Targeted inhibition of transcription elongation in cells mediated by triplex-forming oligonucleotides". Proc Natl Acad Sci U S A. 97 (8): 3862–7. Bibcode:2000PNAS...97.3862F. doi:10.1073/pnas.97.8.3862. PMC 18107. PMID 10760257.
Reddy BS, Sharma SK, Lown JW (2001). "Recent developments in sequence selective minor groove DNA effectors". Curr. Med. Chem. 8 (5): 475–508. doi:10.2174/0929867003373292. PMID 11281837.
Dervan PB (2001). "Molecular Recognition of DNA by Small Molecules". Bioorg. Med. Chem. 9 (9): 2215–2235. doi:10.1016/s0968-0896(01)00262-0. PMID 11553460.
White S, Szewcxyk JW, Turner JM, Baird EE, Dervan PB (1998). "Recognition of the four Watson-Crick base pairs in the DNA minor groove by synthetic ligands" (PDF). Nature. 391 (6666): 468–471. Bibcode:1998Natur.391..468W. doi:10.1038/35106. PMID 9461213. S2CID 205023593.
Dervan PB, Edelson BS (2003). "Recognition of the DNA minor groove by pyrrole-imidazole polyamides". Curr. Opin. Struct. Biol. 13 (3): 284–299. doi:10.1016/s0959-440x(03)00081-2. PMID 12831879.
Trauger JW, Baird EE, Dervan PB (1996). "Recognition of DNA by designed ligands at subnanomolar concentrations". Nature. 382 (6591): 559–561. Bibcode:1996Natur.382..559T. doi:10.1038/382559a0. PMID 8700233. S2CID 4335955.
Wemmer DE (2000). "Designed sequence-specific minor groove ligands". Annu. Rev. Biophys. Biomol. Struct. 29: 439–461. doi:10.1146/annurev.biophys.29.1.439. PMID 10940255.
Kers I, Dervan PB (2002). "Search for the optimal linker in tandem hairpin polyamides". Bioorg. Med. Chem. 10 (10): 3339–3349. doi:10.1016/s0968-0896(02)00221-3. PMID 12150881.
Weyermann P, Dervan PB (2002). "Recognition of ten base pairs of DNA by head-to-head hairpin dimers" (PDF). J. Am. Chem. Soc. 124 (24): 6872–6878. doi:10.1021/ja020258k. PMID 12059208.
Gottesfeld JM, Neely L, Trauger JW, Baird EE, Dervan PB (1997). "Regulation of gene expression by small molecules". Nature. 387 (6629): 202–205. Bibcode:1997Natur.387..202G. doi:10.1038/387202a0. PMID 9144294. S2CID 4358491.
Coull JJ, He G, Melander C, Rucker VC, Dervan PB, Margolis DM (2002). "Targeted derepression of the human immunodeficiency virus type 1 long terminal repeat by pyrrole-imidazole polyamides". J. Virol. 76 (23): 12349–12354. doi:10.1128/jvi.76.23.12349-12354.2002. PMC 136904. PMID 12414976.
Wang YD, Dziegielewski J, Wurtz NR, Dziegielewska B, Dervan PB, Beerman TA (2003). "DNA crosslinking and biological activity of a hairpin polyamide-chlorambucil conjugate". Nucleic Acids Research. 31 (21): 1208–1215. doi:10.1093/nar/gkg215. PMC 150233. PMID 12582240.
Wang YD, Dziegielewski J, Chang AY, Dervan PB, Beerman TA (2002). "Cell-free and cellular activities of a DNA sequence selective hairpin polyamide-CBI conjugate". J. Biol. Chem. 277 (45): 42431–42437. doi:10.1074/jbc.M207179200. PMID 12196541.
Pandian NG, Nakano Y, Sato S, Morinaga H, Bando T, Nagase H, Sugiyama H (2012). "A synthetic small molecule for rapid induction of multiple pluripotency genes in mouse embryonic fibroblasts". Scientific Reports. 2 (544): 544. Bibcode:2012NatSR...2E.544P. doi:10.1038/srep00544. PMC 3408130. PMID 22848790.
Papworth, M.; Kolasinska, P.; Minczuk, M. (January 2006). "Designer zinc-finger proteins and their applications". Gene. 366 (1): 27–38. doi:10.1016/j.gene.2005.09.011. PMID 16298089.
Desjarlais, JR.; Berg, JM. (March 1993). "Use of a zinc-finger consensus sequence framework and specificity rules to design specific DNA binding proteins". Proc Natl Acad Sci U S A. 90 (6): 2256–60. Bibcode:1993PNAS...90.2256D. doi:10.1073/pnas.90.6.2256. PMC 46065. PMID 8460130.
Isalan, M.; Klug, A.; Choo, Y. (July 2001). "A rapid, generally applicable method to engineer zinc fingers illustrated by targeting the HIV-1 promoter". Nat Biotechnol. 19 (7): 656–60. doi:10.1038/90264. PMC 2677679. PMID 11433278.
Choo, Y.; Sánchez-García, I.; Klug, A. (December 1994). "In vivo repression by a site-specific DNA-binding protein designed against an oncogenic sequence" (PDF). Nature. 372 (6507): 642–5. Bibcode:1994Natur.372..642C. doi:10.1038/372642a0. hdl:10261/6295. PMID 7990954. S2CID 12701336.
Carvin, CD.; Parr, RD.; Kladde, MP. (November 2003). "Site-selective in vivo targeting of cytosine-5 DNA methylation by zinc-finger proteins". Nucleic Acids Res. 31 (22): 6493–501. doi:10.1093/nar/gkg853. PMC 275549. PMID 14602907.
Kim, YG.; Cha, J.; Chandrasegaran, S. (February 1996). "Hybrid restriction enzymes: zinc finger fusions to Fok I cleavage domain". Proc Natl Acad Sci U S A. 93 (3): 1156–60. Bibcode:1996PNAS...93.1156K. doi:10.1073/pnas.93.3.1156. PMC 40048. PMID 8577732.
Urnov, FD.; Miller, JC.; Lee, YL.; Beausejour, CM.; Rock, JM.; Augustus, S.; Jamieson, AC.; Porteus, MH.; et al. (June 2005). "Highly efficient endogenous human gene correction using designed zinc-finger nucleases". Nature. 435 (7042): 646–51. Bibcode:2005Natur.435..646U. doi:10.1038/nature03556. PMID 15806097. S2CID 4390010.
Beerli, RR.; Dreier, B.; Barbas, CF. (February 2000). "Positive and negative regulation of endogenous genes by designed transcription factors". Proc Natl Acad Sci U S A. 97 (4): 1495–500. Bibcode:2000PNAS...97.1495B. doi:10.1073/pnas.040552697. PMC 26462. PMID 10660690.
Lara, H.; Wang, Y.; Beltran, AS.; Juárez-Moreno, K.; Yuan, X.; Kato, S.; Leisewitz, AV.; Cuello Fredes, M.; et al. (August 2012). "Targeting serous epithelial ovarian cancer with designer zinc finger transcription factors". J Biol Chem. 287 (35): 29873–86. doi:10.1074/jbc.M112.360768. PMC 3436144. PMID 22782891.
Behlke, MA. (April 2006). "Progress towards in vivo use of siRNAs". Mol Ther. 13 (4): 644–70. doi:10.1016/j.ymthe.2006.01.001. PMC 7106286. PMID 16481219.
Dykxhoorn, DM.; Lieberman, J. (2006). "Running interference: prospects and obstacles to using small interfering RNAs as small molecule drugs". Annu Rev Biomed Eng. 8: 377–402. CiteSeerX 10.1.1.418.758. doi:10.1146/annurev.bioeng.8.061505.095848. PMID 16834561.
Peer, D.; Park, EJ.; Morishita, Y.; Carman, CV.; Shimaoka, M. (February 2008). "Systemic leukocyte-directed siRNA delivery revealing cyclin D1 as an anti-inflammatory target". Science. 319 (5863): 627–30. doi:10.1126/science.1149859. PMC 2490797. PMID 18239128.
Rettig, GR.; Behlke, MA. (March 2012). "Progress toward in vivo use of siRNAs-II". Mol Ther. 20 (3): 483–512. doi:10.1038/mt.2011.263. PMC 3293614. PMID 22186795.
Giacca, M.; Zacchigna, S. (June 2012). "VEGF gene therapy: therapeutic angiogenesis in the clinic and beyond". Gene Ther. 19 (6): 622–9. doi:10.1038/gt.2012.17. PMID 22378343.

handle.net

hdl.handle.net

Choo, Y.; Sánchez-García, I.; Klug, A. (December 1994). "In vivo repression by a site-specific DNA-binding protein designed against an oncogenic sequence" (PDF). Nature. 372 (6507): 642–5. Bibcode:1994Natur.372..642C. doi:10.1038/372642a0. hdl:10261/6295. PMID 7990954. S2CID 12701336.

harvard.edu

ui.adsabs.harvard.edu

Faria, M.; Wood, CD.; Perrouault, L.; Nelson, JS.; Winter, A.; White, MR.; Helene, C.; Giovannangeli, C. (April 2000). "Targeted inhibition of transcription elongation in cells mediated by triplex-forming oligonucleotides". Proc Natl Acad Sci U S A. 97 (8): 3862–7. Bibcode:2000PNAS...97.3862F. doi:10.1073/pnas.97.8.3862. PMC 18107. PMID 10760257.
White S, Szewcxyk JW, Turner JM, Baird EE, Dervan PB (1998). "Recognition of the four Watson-Crick base pairs in the DNA minor groove by synthetic ligands" (PDF). Nature. 391 (6666): 468–471. Bibcode:1998Natur.391..468W. doi:10.1038/35106. PMID 9461213. S2CID 205023593.
Trauger JW, Baird EE, Dervan PB (1996). "Recognition of DNA by designed ligands at subnanomolar concentrations". Nature. 382 (6591): 559–561. Bibcode:1996Natur.382..559T. doi:10.1038/382559a0. PMID 8700233. S2CID 4335955.
Gottesfeld JM, Neely L, Trauger JW, Baird EE, Dervan PB (1997). "Regulation of gene expression by small molecules". Nature. 387 (6629): 202–205. Bibcode:1997Natur.387..202G. doi:10.1038/387202a0. PMID 9144294. S2CID 4358491.
Pandian NG, Nakano Y, Sato S, Morinaga H, Bando T, Nagase H, Sugiyama H (2012). "A synthetic small molecule for rapid induction of multiple pluripotency genes in mouse embryonic fibroblasts". Scientific Reports. 2 (544): 544. Bibcode:2012NatSR...2E.544P. doi:10.1038/srep00544. PMC 3408130. PMID 22848790.
Desjarlais, JR.; Berg, JM. (March 1993). "Use of a zinc-finger consensus sequence framework and specificity rules to design specific DNA binding proteins". Proc Natl Acad Sci U S A. 90 (6): 2256–60. Bibcode:1993PNAS...90.2256D. doi:10.1073/pnas.90.6.2256. PMC 46065. PMID 8460130.
Choo, Y.; Sánchez-García, I.; Klug, A. (December 1994). "In vivo repression by a site-specific DNA-binding protein designed against an oncogenic sequence" (PDF). Nature. 372 (6507): 642–5. Bibcode:1994Natur.372..642C. doi:10.1038/372642a0. hdl:10261/6295. PMID 7990954. S2CID 12701336.
Kim, YG.; Cha, J.; Chandrasegaran, S. (February 1996). "Hybrid restriction enzymes: zinc finger fusions to Fok I cleavage domain". Proc Natl Acad Sci U S A. 93 (3): 1156–60. Bibcode:1996PNAS...93.1156K. doi:10.1073/pnas.93.3.1156. PMC 40048. PMID 8577732.
Urnov, FD.; Miller, JC.; Lee, YL.; Beausejour, CM.; Rock, JM.; Augustus, S.; Jamieson, AC.; Porteus, MH.; et al. (June 2005). "Highly efficient endogenous human gene correction using designed zinc-finger nucleases". Nature. 435 (7042): 646–51. Bibcode:2005Natur.435..646U. doi:10.1038/nature03556. PMID 15806097. S2CID 4390010.
Beerli, RR.; Dreier, B.; Barbas, CF. (February 2000). "Positive and negative regulation of endogenous genes by designed transcription factors". Proc Natl Acad Sci U S A. 97 (4): 1495–500. Bibcode:2000PNAS...97.1495B. doi:10.1073/pnas.040552697. PMC 26462. PMID 10660690.

nih.gov

pubmed.ncbi.nlm.nih.gov

Young WB, Link CJ (2000). "Chimeric retroviral helper virus and picornavirus IRES sequence to eliminate DNA methylation for improved retroviral packaging cells". Journal of Virology. 74 (11): 5242–5249. doi:10.1128/JVI.74.11.5242-5249.2000. PMC 110878. PMID 10799600.
Uil TG, Haisma HJ, Rots MG (2003). "Therapeutic modulation of endogenous gene function by agents with designed DNA-sequence specificities". Nucleic Acids Research. 31 (21): 6064–6078. doi:10.1093/nar/gkg815. PMC 275457. PMID 14576293.
Sargent, RG.; Kim, S.; Gruenert, DC. (2011). "Oligo/polynucleotide-based gene modification: strategies and therapeutic potential". Oligonucleotides. 21 (2): 55–75. doi:10.1089/oli.2010.0273. PMC 3078494. PMID 21417933.
Simon, P.; Cannata, F.; Concordet, JP.; Giovannangeli, C. (August 2008). "Targeting DNA with triplex-forming oligonucleotides to modify gene sequence". Biochimie. 90 (8): 1109–16. doi:10.1016/j.biochi.2008.04.004. PMID 18460344.
Zhou, Y.; Kierzek, E.; Loo, ZP.; Antonio, M.; Yau, YH.; Chuah, YW.; Geifman-Shochat, S.; Kierzek, R.; Chen, G. (July 2013). "Recognition of RNA duplexes by chemically modified triplex-forming oligonucleotides". Nucleic Acids Res. 41 (13): 6664–73. doi:10.1093/nar/gkt352. PMC 3711454. PMID 23658228.
Guntaka, RV.; Varma, BR.; Weber, KT. (January 2003). "Triplex-forming oligonucleotides as modulators of gene expression". Int J Biochem Cell Biol. 35 (1): 22–31. doi:10.1016/s1357-2725(02)00165-6. PMID 12467644.
Faria, M.; Wood, CD.; Perrouault, L.; Nelson, JS.; Winter, A.; White, MR.; Helene, C.; Giovannangeli, C. (April 2000). "Targeted inhibition of transcription elongation in cells mediated by triplex-forming oligonucleotides". Proc Natl Acad Sci U S A. 97 (8): 3862–7. Bibcode:2000PNAS...97.3862F. doi:10.1073/pnas.97.8.3862. PMC 18107. PMID 10760257.
Reddy BS, Sharma SK, Lown JW (2001). "Recent developments in sequence selective minor groove DNA effectors". Curr. Med. Chem. 8 (5): 475–508. doi:10.2174/0929867003373292. PMID 11281837.
Dervan PB (2001). "Molecular Recognition of DNA by Small Molecules". Bioorg. Med. Chem. 9 (9): 2215–2235. doi:10.1016/s0968-0896(01)00262-0. PMID 11553460.
White S, Szewcxyk JW, Turner JM, Baird EE, Dervan PB (1998). "Recognition of the four Watson-Crick base pairs in the DNA minor groove by synthetic ligands" (PDF). Nature. 391 (6666): 468–471. Bibcode:1998Natur.391..468W. doi:10.1038/35106. PMID 9461213. S2CID 205023593.
Dervan PB, Edelson BS (2003). "Recognition of the DNA minor groove by pyrrole-imidazole polyamides". Curr. Opin. Struct. Biol. 13 (3): 284–299. doi:10.1016/s0959-440x(03)00081-2. PMID 12831879.
Lown JW (1988). "Lexitropsins: rational design of DNA sequence reading agents as novel anti-cancer agents and potential cellular probes". Anticancer Drug Des. 3 (1): 25–40. PMID 2838035.
Trauger JW, Baird EE, Dervan PB (1996). "Recognition of DNA by designed ligands at subnanomolar concentrations". Nature. 382 (6591): 559–561. Bibcode:1996Natur.382..559T. doi:10.1038/382559a0. PMID 8700233. S2CID 4335955.
Wemmer DE (2000). "Designed sequence-specific minor groove ligands". Annu. Rev. Biophys. Biomol. Struct. 29: 439–461. doi:10.1146/annurev.biophys.29.1.439. PMID 10940255.
Kers I, Dervan PB (2002). "Search for the optimal linker in tandem hairpin polyamides". Bioorg. Med. Chem. 10 (10): 3339–3349. doi:10.1016/s0968-0896(02)00221-3. PMID 12150881.
Weyermann P, Dervan PB (2002). "Recognition of ten base pairs of DNA by head-to-head hairpin dimers" (PDF). J. Am. Chem. Soc. 124 (24): 6872–6878. doi:10.1021/ja020258k. PMID 12059208.
Gottesfeld JM, Neely L, Trauger JW, Baird EE, Dervan PB (1997). "Regulation of gene expression by small molecules". Nature. 387 (6629): 202–205. Bibcode:1997Natur.387..202G. doi:10.1038/387202a0. PMID 9144294. S2CID 4358491.
Coull JJ, He G, Melander C, Rucker VC, Dervan PB, Margolis DM (2002). "Targeted derepression of the human immunodeficiency virus type 1 long terminal repeat by pyrrole-imidazole polyamides". J. Virol. 76 (23): 12349–12354. doi:10.1128/jvi.76.23.12349-12354.2002. PMC 136904. PMID 12414976.
Wang YD, Dziegielewski J, Wurtz NR, Dziegielewska B, Dervan PB, Beerman TA (2003). "DNA crosslinking and biological activity of a hairpin polyamide-chlorambucil conjugate". Nucleic Acids Research. 31 (21): 1208–1215. doi:10.1093/nar/gkg215. PMC 150233. PMID 12582240.
Wang YD, Dziegielewski J, Chang AY, Dervan PB, Beerman TA (2002). "Cell-free and cellular activities of a DNA sequence selective hairpin polyamide-CBI conjugate". J. Biol. Chem. 277 (45): 42431–42437. doi:10.1074/jbc.M207179200. PMID 12196541.
Pandian NG, Nakano Y, Sato S, Morinaga H, Bando T, Nagase H, Sugiyama H (2012). "A synthetic small molecule for rapid induction of multiple pluripotency genes in mouse embryonic fibroblasts". Scientific Reports. 2 (544): 544. Bibcode:2012NatSR...2E.544P. doi:10.1038/srep00544. PMC 3408130. PMID 22848790.
Papworth, M.; Kolasinska, P.; Minczuk, M. (January 2006). "Designer zinc-finger proteins and their applications". Gene. 366 (1): 27–38. doi:10.1016/j.gene.2005.09.011. PMID 16298089.
Desjarlais, JR.; Berg, JM. (March 1993). "Use of a zinc-finger consensus sequence framework and specificity rules to design specific DNA binding proteins". Proc Natl Acad Sci U S A. 90 (6): 2256–60. Bibcode:1993PNAS...90.2256D. doi:10.1073/pnas.90.6.2256. PMC 46065. PMID 8460130.
Isalan, M.; Klug, A.; Choo, Y. (July 2001). "A rapid, generally applicable method to engineer zinc fingers illustrated by targeting the HIV-1 promoter". Nat Biotechnol. 19 (7): 656–60. doi:10.1038/90264. PMC 2677679. PMID 11433278.
Choo, Y.; Sánchez-García, I.; Klug, A. (December 1994). "In vivo repression by a site-specific DNA-binding protein designed against an oncogenic sequence" (PDF). Nature. 372 (6507): 642–5. Bibcode:1994Natur.372..642C. doi:10.1038/372642a0. hdl:10261/6295. PMID 7990954. S2CID 12701336.
Carvin, CD.; Parr, RD.; Kladde, MP. (November 2003). "Site-selective in vivo targeting of cytosine-5 DNA methylation by zinc-finger proteins". Nucleic Acids Res. 31 (22): 6493–501. doi:10.1093/nar/gkg853. PMC 275549. PMID 14602907.
Kim, YG.; Cha, J.; Chandrasegaran, S. (February 1996). "Hybrid restriction enzymes: zinc finger fusions to Fok I cleavage domain". Proc Natl Acad Sci U S A. 93 (3): 1156–60. Bibcode:1996PNAS...93.1156K. doi:10.1073/pnas.93.3.1156. PMC 40048. PMID 8577732.
Urnov, FD.; Miller, JC.; Lee, YL.; Beausejour, CM.; Rock, JM.; Augustus, S.; Jamieson, AC.; Porteus, MH.; et al. (June 2005). "Highly efficient endogenous human gene correction using designed zinc-finger nucleases". Nature. 435 (7042): 646–51. Bibcode:2005Natur.435..646U. doi:10.1038/nature03556. PMID 15806097. S2CID 4390010.
Beerli, RR.; Dreier, B.; Barbas, CF. (February 2000). "Positive and negative regulation of endogenous genes by designed transcription factors". Proc Natl Acad Sci U S A. 97 (4): 1495–500. Bibcode:2000PNAS...97.1495B. doi:10.1073/pnas.040552697. PMC 26462. PMID 10660690.
Lara, H.; Wang, Y.; Beltran, AS.; Juárez-Moreno, K.; Yuan, X.; Kato, S.; Leisewitz, AV.; Cuello Fredes, M.; et al. (August 2012). "Targeting serous epithelial ovarian cancer with designer zinc finger transcription factors". J Biol Chem. 287 (35): 29873–86. doi:10.1074/jbc.M112.360768. PMC 3436144. PMID 22782891.
Snowden, AW.; Zhang, L.; Urnov, F.; Dent, C.; Jouvenot, Y.; Zhong, X.; Rebar, EJ.; Jamieson, AC.; et al. (December 2003). "Repression of vascular endothelial growth factor A in glioblastoma cells using engineered zinc finger transcription factors". Cancer Res. 63 (24): 8968–76. PMID 14695215.
Behlke, MA. (April 2006). "Progress towards in vivo use of siRNAs". Mol Ther. 13 (4): 644–70. doi:10.1016/j.ymthe.2006.01.001. PMC 7106286. PMID 16481219.
Dykxhoorn, DM.; Lieberman, J. (2006). "Running interference: prospects and obstacles to using small interfering RNAs as small molecule drugs". Annu Rev Biomed Eng. 8: 377–402. CiteSeerX 10.1.1.418.758. doi:10.1146/annurev.bioeng.8.061505.095848. PMID 16834561.
Peer, D.; Park, EJ.; Morishita, Y.; Carman, CV.; Shimaoka, M. (February 2008). "Systemic leukocyte-directed siRNA delivery revealing cyclin D1 as an anti-inflammatory target". Science. 319 (5863): 627–30. doi:10.1126/science.1149859. PMC 2490797. PMID 18239128.
Rettig, GR.; Behlke, MA. (March 2012). "Progress toward in vivo use of siRNAs-II". Mol Ther. 20 (3): 483–512. doi:10.1038/mt.2011.263. PMC 3293614. PMID 22186795.
Giacca, M.; Zacchigna, S. (June 2012). "VEGF gene therapy: therapeutic angiogenesis in the clinic and beyond". Gene Ther. 19 (6): 622–9. doi:10.1038/gt.2012.17. PMID 22378343.

ncbi.nlm.nih.gov

Young WB, Link CJ (2000). "Chimeric retroviral helper virus and picornavirus IRES sequence to eliminate DNA methylation for improved retroviral packaging cells". Journal of Virology. 74 (11): 5242–5249. doi:10.1128/JVI.74.11.5242-5249.2000. PMC 110878. PMID 10799600.
Uil TG, Haisma HJ, Rots MG (2003). "Therapeutic modulation of endogenous gene function by agents with designed DNA-sequence specificities". Nucleic Acids Research. 31 (21): 6064–6078. doi:10.1093/nar/gkg815. PMC 275457. PMID 14576293.
Sargent, RG.; Kim, S.; Gruenert, DC. (2011). "Oligo/polynucleotide-based gene modification: strategies and therapeutic potential". Oligonucleotides. 21 (2): 55–75. doi:10.1089/oli.2010.0273. PMC 3078494. PMID 21417933.
Zhou, Y.; Kierzek, E.; Loo, ZP.; Antonio, M.; Yau, YH.; Chuah, YW.; Geifman-Shochat, S.; Kierzek, R.; Chen, G. (July 2013). "Recognition of RNA duplexes by chemically modified triplex-forming oligonucleotides". Nucleic Acids Res. 41 (13): 6664–73. doi:10.1093/nar/gkt352. PMC 3711454. PMID 23658228.
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