유전자 치료 (Korean Wikipedia)

Analysis of information sources in references of the Wikipedia article "유전자 치료" in Korean language version.

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abedia.com

Gene Therapy Clinical Trials Worldwide Database Archived 2017년 7월 15일 - 웨이백 머신. The Journal of Gene Medicine. Wiley (June 2016)

allfordrugs.com

Crasto AM (2013년 7월 7일). “Glybera – The Most Expensive Drug in the world & First Approved Gene Therapy in the West”. 《All About Drugs》. 2013년 11월 2일에 확인함.
Crasto AM (2013년 7월 7일). “Glybera – The Most Expensive Drug in the world & First Approved Gene Therapy in the West”. 《All About Drugs》. 2013년 11월 2일에 확인함.

ama-assn.org

“Gene Therapy”. 《ama-assn.org》. 2014년 4월 4일. 2015년 3월 15일에 원본 문서에서 보존된 문서. 2015년 3월 22일에 확인함.

arhp.org

“Human Cloning and Genetic Modification”. Association of Reproductive Health Officials. 2013. 2013년 6월 18일에 원본 문서에서 보존된 문서.

bbc.co.uk

Ghosh P (2016년 4월 28일). “Gene therapy reverses sight loss and is long-lasting”. BBC News, Science & Environment. 2016년 4월 29일에 확인함.
Gallagher, James. (2 November 2012) BBC News – Gene therapy: Glybera approved by European Commission. BBC. Retrieved 15 December 2012.
Gallagher, James (21 April 2015) Gene therapy: 'Tame HIV' used to cure disease BBC News, Health, Retrieved 21 April 2015
Walsh F (2015년 12월 3일). “Gene editing: Is era of designer humans getting closer?”. BBC News Health. 2015년 12월 31일에 확인함.

news.bbc.co.uk

“Gene therapy first for poor sight”. BBC News. 2007년 5월 1일. 2010년 5월 3일에 확인함.

bionews.org.uk

“Gene therapy approved in Europe for first time”. 2017년 9월 13일에 원본 문서에서 보존된 문서. 2018년 4월 24일에 확인함.
Reeves R (2016년 6월 6일). “Second gene therapy wins approval in Europe”. 《Bionews》. 2017년 2월 21일에 원본 문서에서 보존된 문서. 2017년 2월 20일에 확인함.

books.google.com

U.S. Congress, Office of Technology Assessment (December 1984). 《Human gene therapy – A background paper》. DIANE Publishing. ISBN 978-1-4289-2371-3.
Lowenstein PR (2008). 〈Gene Therapy for Neurological Disorders: New Therapies or Human Experimentation?〉. Burley J, Harris J. 《A Companion to Genethics》. John Wiley & Sons. ISBN 978-0-470-75637-9.

bostonglobe.com

“Ten things you might have missed Monday from the world of business”. 《Boston Globe》. 2015년 2월 3일. 2015년 2월 13일에 확인함.

celladon.com

ir.celladon.com

Celladon Receives Breakthrough Therapy Designation From FDA for MYDICAR(R), Novel, First-in-Class Therapy in Development to Treat Heart Failure Archived 2015년 7월 10일 - 웨이백 머신. New York Times (10 April 2014)

clinicaltrials.gov

Clinical trial number NCT01639690 for "β-Thalassemia Major With Autologous CD34+ Hematopoietic Progenitor Cells Transduced With TNS9.3.55 a Lentiviral Vector Encoding the Normal Human β-Globin Gene" - ClinicalTrials.gov
Clinical trial number NCT02247843 for "Stem Cell Gene Therapy for Sickle Cell Disease" - ClinicalTrials.gov
Clinical trial number NCT00012545 for "Collection and Storage of Umbilical Cord Stem Cells for Treatment of Sickle Cell Disease" - ClinicalTrials.gov

dddmag.com

“Gene Therapy for PAD Approved”. 2011년 12월 6일. 2015년 8월 5일에 확인함.

dnapolicy.org

“International Law”. The Genetics and Public Policy Center, Johns Hopkins University Berman Institute of Bioethics. 2010. 2 September 2014에 원본 문서에서 보존된 문서.

doi.org

dx.doi.org

Kaji, Eugene H. (2001년 2월 7일). “Gene and Stem Cell Therapies”. 《JAMA》 (영어) 285 (5). doi:10.1001/jama.285.5.545. ISSN 0098-7484. ^{[깨진 링크(과거 내용 찾기)]}
Sun M (October 1982). “Martin Cline loses appeal on NIH grant”. 《Science》 218 (4567): 37. doi:10.1126/science.7123214. PMID 7123214.
Sheridan C (February 2011). “Gene therapy finds its niche”. 《Nature Biotechnology》 29 (2): 121–8. doi:10.1038/nbt.1769. PMID 21301435.
Maguire AM, Simonelli F, Pierce EA, Pugh EN, Mingozzi F, Bennicelli J, 외. (May 2008). “Safety and efficacy of gene transfer for Leber's congenital amaurosis”. 《The New England Journal of Medicine》 358 (21): 2240–8. doi:10.1056/NEJMoa0802315. PMC 2829748. PMID 18441370.
Simonelli F, Maguire AM, Testa F, Pierce EA, Mingozzi F, Bennicelli JL, 외. (March 2010). “Gene therapy for Leber's congenital amaurosis is safe and effective through 1.5 years after vector administration”. 《Molecular Therapy》 18 (3): 643–50. doi:10.1038/mt.2009.277. PMC 2839440. PMID 19953081.
Cideciyan AV, Hauswirth WW, Aleman TS, Kaushal S, Schwartz SB, Boye SL, Windsor EA, Conlon TJ, Sumaroka A, Roman AJ, Byrne BJ, Jacobson SG (August 2009). “Vision 1 year after gene therapy for Leber's congenital amaurosis”. 《The New England Journal of Medicine》 361 (7): 725–7. doi:10.1056/NEJMc0903652. PMC 2847775. PMID 19675341.
Bainbridge JW, Smith AJ, Barker SS, Robbie S, Henderson R, Balaggan K, 외. (May 2008). “Effect of gene therapy on visual function in Leber's congenital amaurosis”. 《The New England Journal of Medicine》 358 (21): 2231–9. doi:10.1056/NEJMoa0802268. PMID 18441371.
Fischer A, Hacein-Bey-Abina S, Cavazzana-Calvo M (June 2010). “20 years of gene therapy for SCID”. 《Nature Immunology》 11 (6): 457–60. doi:10.1038/ni0610-457. PMID 20485269.
Ferrua F, Brigida I, Aiuti A (December 2010). “Update on gene therapy for adenosine deaminase-deficient severe combined immunodeficiency”. 《Current Opinion in Allergy and Clinical Immunology》 10 (6): 551–6. doi:10.1097/ACI.0b013e32833fea85. PMID 20966749.
Cartier N, Aubourg P (July 2010). “Hematopoietic stem cell transplantation and hematopoietic stem cell gene therapy in X-linked adrenoleukodystrophy”. 《Brain Pathology》 20 (4): 857–62. doi:10.1111/j.1750-3639.2010.00394.x. PMID 20626747.
Ledford H (2011). “Cell therapy fights leukaemia”. 《Nature》. doi:10.1038/news.2011.472.
LeWitt PA, Rezai AR, Leehey MA, Ojemann SG, Flaherty AW, Eskandar EN, 외. (April 2011). “AAV2-GAD gene therapy for advanced Parkinson's disease: a double-blind, sham-surgery controlled, randomised trial”. 《The Lancet. Neurology》 10 (4): 309–19. doi:10.1016/S1474-4422(11)70039-4. PMID 21419704.
Pearson S, Jia H, Kandachi K (January 2004). “China approves first gene therapy”. 《Nature Biotechnology》 22 (1): 3–4. doi:10.1038/nbt0104-3. PMID 14704685.
Pezzoli D, Chiesa R, De Nardo L, Candiani G (September 2012). “We still have a long way to go to effectively deliver genes!”. 《Journal of Applied Biomaterials & Functional Materials》 10 (2): 82–91. doi:10.5301/JABFM.2012.9707. PMID 23015375.
Urnov FD, Rebar EJ, Holmes MC, Zhang HS, Gregory PD (September 2010). “Genome editing with engineered zinc finger nucleases”. 《Nature Reviews Genetics》 11 (9): 636–46. doi:10.1038/nrg2842. PMID 20717154.
Mavilio F, Ferrari G (July 2008). “Genetic modification of somatic stem cells. The progress, problems and prospects of a new therapeutic technology”. 《EMBO Reports》. 9 Suppl 1: S64–9. doi:10.1038/embor.2008.81. PMC 3327547. PMID 18578029.
Mullard, Asher (2020년 5월 15일). “Gene-editing pipeline takes off”. 《Nature Reviews Drug Discovery》 (영어) 19 (6): 367–372. doi:10.1038/d41573-020-00096-y.
Woods NB, Bottero V, Schmidt M, von Kalle C, Verma IM (April 2006). “Gene therapy: therapeutic gene causing lymphoma”. 《Nature》 440 (7088): 1123. Bibcode:2006Natur.440.1123W. doi:10.1038/4401123a. PMID 16641981.
Thrasher AJ, Gaspar HB, Baum C, Modlich U, Schambach A, Candotti F, 외. (September 2006). “Gene therapy: X-SCID transgene leukaemogenicity”. 《Nature》 443 (7109): E5–6; discussion E6–7. Bibcode:2006Natur.443E...5T. doi:10.1038/nature05219. PMID 16988659.
Friedmann T, Roblin R (March 1972). “Gene therapy for human genetic disease?”. 《Science》 175 (4025): 949–55. Bibcode:1972Sci...175..949F. doi:10.1126/science.175.4025.949. PMID 5061866.
Cepko CL, Roberts BE, Mulligan RC (July 1984). “Construction and applications of a highly transmissible murine retrovirus shuttle vector”. 《Cell》 37 (3): 1053–62. doi:10.1016/0092-8674(84)90440-9. PMID 6331674.
Blaese RM, Culver KW, Miller AD, Carter CS, Fleisher T, Clerici M, 외. (October 1995). “T lymphocyte-directed gene therapy for ADA- SCID: initial trial results after 4 years”. 《Science》 270 (5235): 475–80. Bibcode:1995Sci...270..475B. doi:10.1126/science.270.5235.475. PMID 7570001.
Trojan J, Johnson TR, Rudin SD, Ilan J, Tykocinski ML, Ilan J (January 1993). “Treatment and prevention of rat glioblastoma by immunogenic C6 cells expressing antisense insulin-like growth factor I RNA”. 《Science》 259 (5091): 94–7. Bibcode:1993Sci...259...94T. doi:10.1126/science.8418502. PMID 8418502.
Trojan J, Pan YX, Wei MX, Ly A, Shevelev A, Bierwagen M, 외. (2012). “Methodology for Anti-Gene Anti-IGF-I Therapy of Malignant Tumours”. 《Chemotherapy Research and Practice》 2012: 721873. doi:10.1155/2012/721873. PMC 3287029. PMID 22400112.
Abbott A (April 1992). “Gene therapy. Italians first to use stem cells”. 《Nature》 356 (6369): 465. Bibcode:1992Natur.356..465A. doi:10.1038/356465a0. PMID 1560817.
Cavazzana-Calvo M, Thrasher A, Mavilio F (February 2004). “The future of gene therapy”. 《Nature》 427 (6977): 779–81. Bibcode:2004Natur.427..779C. doi:10.1038/427779a. PMID 14985734.
Ott MG, Schmidt M, Schwarzwaelder K, Stein S, Siler U, Koehl U, 외. (April 2006). “Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1”. 《Nature Medicine》 12 (4): 401–9. doi:10.1038/nm1393. PMID 16582916.
Brown BD, Venneri MA, Zingale A, Sergi Sergi L, Naldini L (May 2006). “Endogenous microRNA regulation suppresses transgene expression in hematopoietic lineages and enables stable gene transfer”. 《Nature Medicine》 12 (5): 585–91. doi:10.1038/nm1398. PMID 16633348.
Morgan RA, Dudley ME, Wunderlich JR, Hughes MS, Yang JC, Sherry RM, 외. (October 2006). “Cancer regression in patients after transfer of genetically engineered lymphocytes”. 《Science》 314 (5796): 126–9. Bibcode:2006Sci...314..126M. doi:10.1126/science.1129003. PMC 2267026. PMID 16946036.
Levine BL, Humeau LM, Boyer J, MacGregor RR, Rebello T, Lu X, 외. (November 2006). “Gene transfer in humans using a conditionally replicating lentiviral vector”. 《Proceedings of the National Academy of Sciences of the United States of America》 103 (46): 17372–7. Bibcode:2006PNAS..10317372L. doi:10.1073/pnas.0608138103. PMC 1635018. PMID 17090675.
Dolgin E (2009). “Colour blindness corrected by gene therapy”. 《Nature》. doi:10.1038/news.2009.921.
Cartier N, Hacein-Bey-Abina S, Bartholomae CC, Veres G, Schmidt M, Kutschera I, 외. (November 2009). “Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy”. 《Science》 326 (5954): 818–23. Bibcode:2009Sci...326..818C. doi:10.1126/science.1171242. PMID 19892975.
Komáromy AM, Alexander JJ, Rowlan JS, Garcia MM, Chiodo VA, Kaya A, 외. (July 2010). “Gene therapy rescues cone function in congenital achromatopsia”. 《Human Molecular Genetics》 19 (13): 2581–93. doi:10.1093/hmg/ddq136. PMC 2883338. PMID 20378608.
Cavazzana-Calvo M, Payen E, Negre O, Wang G, Hehir K, Fusil F, 외. (September 2010). “Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia”. 《Nature》 467 (7313): 318–22. Bibcode:2010Natur.467..318C. doi:10.1038/nature09328. PMC 3355472. PMID 20844535.
Yang ZJ, Zhang YR, Chen B, Zhang SL, Jia EZ, Wang LS, 외. (July 2009). “Phase I clinical trial on intracoronary administration of Ad-hHGF treating severe coronary artery disease”. 《Molecular Biology Reports》 36 (6): 1323–9. doi:10.1007/s11033-008-9315-3. PMID 18649012.
Hahn W, Pyun WB, Kim DS, Yoo WS, Lee SD, Won JH, 외. (October 2011). “Enhanced cardioprotective effects by coexpression of two isoforms of hepatocyte growth factor from naked plasmid DNA in a rat ischemic heart disease model”. 《The Journal of Gene Medicine》 13 (10): 549–55. doi:10.1002/jgm.1603. PMID 21898720.
Deev RV, Bozo IY, Mzhavanadze ND, Voronov DA, Gavrilenko AV, Chervyakov YV, 외. (September 2015). “pCMV-vegf165 Intramuscular Gene Transfer is an Effective Method of Treatment for Patients With Chronic Lower Limb Ischemia”. 《Journal of Cardiovascular Pharmacology and Therapeutics》 20 (5): 473–82. doi:10.1177/1074248415574336. PMID 25770117.
Fernàndez-Ruiz I (March 2016). “Gene therapy: No improvement in outcomes with gene therapy for heart failure”. 《Nature Reviews. Cardiology》 13 (3): 122–3. doi:10.1038/nrcardio.2016.14. PMID 26843287.
Biffi A, Montini E, Lorioli L, Cesani M, Fumagalli F, Plati T, 외. (August 2013). “Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy”. 《Science》 341 (6148): 1233158. doi:10.1126/science.1233158. PMID 23845948.
Aiuti A, Biasco L, Scaramuzza S, Ferrua F, Cicalese MP, Baricordi C, 외. (August 2013). “Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome”. 《Science》 341 (6148): 1233151. doi:10.1126/science.1233151. PMC 4375961. PMID 23845947.
Malech HL, Ochs HD (April 2015). “An emerging era of clinical benefit from gene therapy”. 《JAMA》 313 (15): 1522–3. doi:10.1001/jama.2015.2055. PMID 25898049.
MacLaren RE, Groppe M, Barnard AR, Cottriall CL, Tolmachova T, Seymour L, Clark KR, During MJ, Cremers FP, Black GC, Lotery AJ, Downes SM, Webster AR, Seabra MC (March 2014). “Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial”. 《Lancet》 383 (9923): 1129–37. doi:10.1016/S0140-6736(13)62117-0. PMC 4171740. PMID 24439297.
Tebas P, Stein D, Tang WW, Frank I, Wang SQ, Lee G, 외. (March 2014). “Gene editing of CCR5 in autologous CD4 T cells of persons infected with HIV”. 《The New England Journal of Medicine》 370 (10): 901–10. doi:10.1056/NEJMoa1300662. PMC 4084652. PMID 24597865.
Olowoyeye A, Okwundu CI (November 2016). “Gene therapy for sickle cell disease”. 《The Cochrane Database of Systematic Reviews》 11: CD007652. doi:10.1002/14651858.CD007652.pub5. PMID 27841932.
Gardner MR, Kattenhorn LM, Kondur HR, von Schaewen M, Dorfman T, Chiang JJ, 외. (March 2015). “AAV-expressed eCD4-Ig provides durable protection from multiple SHIV challenges”. 《Nature》 519 (7541): 87–91. Bibcode:2015Natur.519...87G. doi:10.1038/nature14264. PMC 4352131. PMID 25707797.
Baltimore D, Berg P, Botchan M, Carroll D, Charo RA, Church G, 외. (April 2015). “Biotechnology. A prudent path forward for genomic engineering and germline gene modification”. 《Science》 348 (6230): 36–8. Bibcode:2015Sci...348...36B. doi:10.1126/science.aab1028. PMC 4394183. PMID 25791083.
Lanphier E, Urnov F, Haecker SE, Werner M, Smolenski J (March 2015). “Don't edit the human germ line”. 《Nature》 519 (7544): 410–1. Bibcode:2015Natur.519..410L. doi:10.1038/519410a. PMID 25810189.
Cyranoski D (July 2016). “Chinese scientists to pioneer first human CRISPR trial”. 《Nature》 535 (7613): 476–7. doi:10.1038/nature.2016.20302. PMID 27466105.
Lee TW, Southern KW, Perry LA, Penny-Dimri JC, Aslam AA (June 2016). “Topical cystic fibrosis transmembrane conductance regulator gene replacement for cystic fibrosis-related lung disease”. 《The Cochrane Database of Systematic Reviews》 (6): CD005599. doi:10.1002/14651858.CD005599.pub5. PMID 27314455.
Rangarajan S, Walsh L, Lester W, Perry D, Madan B, Laffan M, 외. (December 2017). “AAV5-Factor VIII Gene Transfer in Severe Hemophilia A”. 《The New England Journal of Medicine》 377 (26): 2519–2530. doi:10.1056/nejmoa1708483. PMID 29224506.
van den Berg HM (December 2017). “A Cure for Hemophilia within Reach”. 《The New England Journal of Medicine》 377 (26): 2592–2593. doi:10.1056/nejme1713888. PMID 29224412.
Liang P, Xu Y, Zhang X, Ding C, Huang R, Zhang Z, Lv J, Xie X, Chen Y, Li Y, Sun Y, Bai Y, Songyang Z, Ma W, Zhou C, Huang J (May 2015). “CRISPR/Cas9-mediated gene editing in human tripronuclear zygotes”. 《Protein & Cell》 6 (5): 363–372. doi:10.1007/s13238-015-0153-5. PMC 4417674. PMID 25894090.
Wu Y, Zhou H, Fan X, Zhang Y, Zhang M, Wang Y, 외. (January 2015). “Correction of a genetic disease by CRISPR-Cas9-mediated gene editing in mouse spermatogonial stem cells”. 《Cell Research》 25 (1): 67–79. doi:10.1038/cr.2014.160. PMC 4650588. PMID 25475058.
Powell R, Buchanan A (February 2011). “Breaking evolution's chains: the prospect of deliberate genetic modification in humans”. 《The Journal of Medicine and Philosophy》 36 (1): 6–27. doi:10.1093/jmp/jhq057. PMID 21228084.
Baylis F, Robert JS (2004). “The inevitability of genetic enhancement technologies”. 《Bioethics》 18 (1): 1–26. doi:10.1111/j.1467-8519.2004.00376.x. PMID 15168695.
“Ethical issues related to prenatal genetic testing. The Council on Ethical and Judicial Affairs, American Medical Association”. 《Archives of Family Medicine》 3 (7): 633–42. July 1994. doi:10.1001/archfami.3.7.633. PMID 7921302.
Smith KR, Chan S, Harris J (October 2012). “Human germline genetic modification: scientific and bioethical perspectives”. 《Archives of Medical Research》 43 (7): 491–513. doi:10.1016/j.arcmed.2012.09.003. PMID 23072719.
Reardon S (2017년 2월 14일). “US science advisers outline path to genetically modified babies”. 《Nature》. doi:10.1038/nature.2017.21474.

doi.org

Allessandra Biffi(2013). "Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy" Science 341(6148) doi: 10.1126/science.1233158
Florian Eichler(2017). "Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy" The New England Journal of Medicine 377:1630-1638 DOI: 10.1056/NEJMoa1700554
Zhanhui Ou(2016). "The Combination of CRISPR/Cas9 and iPSC Technologies in the Gene Therapy of Human β-thalassemia in Mice" Scientific Reports 6:32463 doi:10.1038/srep32463
Juli R. Bagó(2016). "Therapeutically engineered induced neural stem cells are tumour-homing and inhibit progression of glioblastoma" Nature Communications 7:10593 doi: 10.1038/ncomms10593
Ryosuke Uchibori(2014). "Cancer gene therapy using mesenchymal stem cells" International Journal of Hematology 99(4): 377-82 https://doi.org/10.1007/s12185-014-1537-7

eurekalert.org

“Penn Medicine presents HIV gene therapy trial data at CROI 2009”. EurekAlert!. 2009년 2월 10일. 2012년 8월 25일에 원본 문서에서 보존된 문서. 2009년 11월 19일에 확인함.

eurolab.ua

Eurolab. Neovasculogen listing in Eurolab Page accessed 4 August 2015

europa.eu

ema.europa.eu

“Summary of opinion1 (initial authorisation) Strimvelis” (PDF). 《European Medicines Agency》. 2016년 4월 1일. 1–2쪽. 2018년 1월 28일에 원본 문서 (PDF)에서 보존된 문서. 2016년 4월 13일에 확인함.

fda.gov

“FDA approval brings first gene therapy to the United States”. 《FDA News Release》. U.S. Food and Drug Administration. 2017년 8월 30일.
Research, Center for Drug Evaluation and. “Approved Drugs - FDA approves axicabtagene ciloleucel for large B-cell lymphoma”. 《www.fda.gov》 (영어). 2018년 1월 5일에 확인함.
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forbes.com

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