Lowenstein PR (2008). 〈Gene Therapy for Neurological Disorders: New Therapies or Human Experimentation?〉. Burley J, Harris J. 《A Companion to Genethics》. John Wiley & Sons. ISBN978-0-470-75637-9.
Clinical trial number NCT01639690 for "β-Thalassemia Major With Autologous CD34+ Hematopoietic Progenitor Cells Transduced With TNS9.3.55 a Lentiviral Vector Encoding the Normal Human β-Globin Gene" - ClinicalTrials.gov
“International Law”. The Genetics and Public Policy Center, Johns Hopkins University Berman Institute of Bioethics. 2010. 2 September 2014에 원본 문서에서 보존된 문서.
Bainbridge JW, Smith AJ, Barker SS, Robbie S, Henderson R, Balaggan K, 외. (May 2008). “Effect of gene therapy on visual function in Leber's congenital amaurosis”. 《The New England Journal of Medicine》 358 (21): 2231–9. doi:10.1056/NEJMoa0802268. PMID18441371.
Fischer A, Hacein-Bey-Abina S, Cavazzana-Calvo M (June 2010). “20 years of gene therapy for SCID”. 《Nature Immunology》 11 (6): 457–60. doi:10.1038/ni0610-457. PMID20485269.
Ferrua F, Brigida I, Aiuti A (December 2010). “Update on gene therapy for adenosine deaminase-deficient severe combined immunodeficiency”. 《Current Opinion in Allergy and Clinical Immunology》 10 (6): 551–6. doi:10.1097/ACI.0b013e32833fea85. PMID20966749.
Cartier N, Aubourg P (July 2010). “Hematopoietic stem cell transplantation and hematopoietic stem cell gene therapy in X-linked adrenoleukodystrophy”. 《Brain Pathology》 20 (4): 857–62. doi:10.1111/j.1750-3639.2010.00394.x. PMID20626747.
LeWitt PA, Rezai AR, Leehey MA, Ojemann SG, Flaherty AW, Eskandar EN, 외. (April 2011). “AAV2-GAD gene therapy for advanced Parkinson's disease: a double-blind, sham-surgery controlled, randomised trial”. 《The Lancet. Neurology》 10 (4): 309–19. doi:10.1016/S1474-4422(11)70039-4. PMID21419704.
Pearson S, Jia H, Kandachi K (January 2004). “China approves first gene therapy”. 《Nature Biotechnology》 22 (1): 3–4. doi:10.1038/nbt0104-3. PMID14704685.
Pezzoli D, Chiesa R, De Nardo L, Candiani G (September 2012). “We still have a long way to go to effectively deliver genes!”. 《Journal of Applied Biomaterials & Functional Materials》 10 (2): 82–91. doi:10.5301/JABFM.2012.9707. PMID23015375.
Cepko CL, Roberts BE, Mulligan RC (July 1984). “Construction and applications of a highly transmissible murine retrovirus shuttle vector”. 《Cell》 37 (3): 1053–62. doi:10.1016/0092-8674(84)90440-9. PMID6331674.
Blaese RM, Culver KW, Miller AD, Carter CS, Fleisher T, Clerici M, 외. (October 1995). “T lymphocyte-directed gene therapy for ADA- SCID: initial trial results after 4 years”. 《Science》 270 (5235): 475–80. Bibcode:1995Sci...270..475B. doi:10.1126/science.270.5235.475. PMID7570001.
Trojan J, Johnson TR, Rudin SD, Ilan J, Tykocinski ML, Ilan J (January 1993). “Treatment and prevention of rat glioblastoma by immunogenic C6 cells expressing antisense insulin-like growth factor I RNA”. 《Science》 259 (5091): 94–7. Bibcode:1993Sci...259...94T. doi:10.1126/science.8418502. PMID8418502.
Dolgin E (2009). “Colour blindness corrected by gene therapy”. 《Nature》. doi:10.1038/news.2009.921.
Cartier N, Hacein-Bey-Abina S, Bartholomae CC, Veres G, Schmidt M, Kutschera I, 외. (November 2009). “Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy”. 《Science》 326 (5954): 818–23. Bibcode:2009Sci...326..818C. doi:10.1126/science.1171242. PMID19892975.
Yang ZJ, Zhang YR, Chen B, Zhang SL, Jia EZ, Wang LS, 외. (July 2009). “Phase I clinical trial on intracoronary administration of Ad-hHGF treating severe coronary artery disease”. 《Molecular Biology Reports》 36 (6): 1323–9. doi:10.1007/s11033-008-9315-3. PMID18649012.
Hahn W, Pyun WB, Kim DS, Yoo WS, Lee SD, Won JH, 외. (October 2011). “Enhanced cardioprotective effects by coexpression of two isoforms of hepatocyte growth factor from naked plasmid DNA in a rat ischemic heart disease model”. 《The Journal of Gene Medicine》 13 (10): 549–55. doi:10.1002/jgm.1603. PMID21898720.
Deev RV, Bozo IY, Mzhavanadze ND, Voronov DA, Gavrilenko AV, Chervyakov YV, 외. (September 2015). “pCMV-vegf165 Intramuscular Gene Transfer is an Effective Method of Treatment for Patients With Chronic Lower Limb Ischemia”. 《Journal of Cardiovascular Pharmacology and Therapeutics》 20 (5): 473–82. doi:10.1177/1074248415574336. PMID25770117.
Fernàndez-Ruiz I (March 2016). “Gene therapy: No improvement in outcomes with gene therapy for heart failure”. 《Nature Reviews. Cardiology》 13 (3): 122–3. doi:10.1038/nrcardio.2016.14. PMID26843287.
Biffi A, Montini E, Lorioli L, Cesani M, Fumagalli F, Plati T, 외. (August 2013). “Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy”. 《Science》 341 (6148): 1233158. doi:10.1126/science.1233158. PMID23845948.
Olowoyeye A, Okwundu CI (November 2016). “Gene therapy for sickle cell disease”. 《The Cochrane Database of Systematic Reviews》 11: CD007652. doi:10.1002/14651858.CD007652.pub5. PMID27841932.
Powell R, Buchanan A (February 2011). “Breaking evolution's chains: the prospect of deliberate genetic modification in humans”. 《The Journal of Medicine and Philosophy》 36 (1): 6–27. doi:10.1093/jmp/jhq057. PMID21228084.
Florian Eichler(2017). "Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy" The New England Journal of Medicine377:1630-1638 DOI: 10.1056/NEJMoa1700554
Zhanhui Ou(2016). "The Combination of CRISPR/Cas9 and iPSC Technologies in the Gene Therapy of Human β-thalassemia in Mice" Scientific Reports6:32463 doi:10.1038/srep32463
Juli R. Bagó(2016). "Therapeutically engineered induced neural stem cells are tumour-homing and inhibit progression of glioblastoma" Nature Communications7:10593 doi: 10.1038/ncomms10593
Ryosuke Uchibori(2014). "Cancer gene therapy using mesenchymal stem cells" International Journal of Hematology99(4): 377-82 https://doi.org/10.1007/s12185-014-1537-7
Blaese RM, Culver KW, Miller AD, Carter CS, Fleisher T, Clerici M, 외. (October 1995). “T lymphocyte-directed gene therapy for ADA- SCID: initial trial results after 4 years”. 《Science》 270 (5235): 475–80. Bibcode:1995Sci...270..475B. doi:10.1126/science.270.5235.475. PMID7570001.
Trojan J, Johnson TR, Rudin SD, Ilan J, Tykocinski ML, Ilan J (January 1993). “Treatment and prevention of rat glioblastoma by immunogenic C6 cells expressing antisense insulin-like growth factor I RNA”. 《Science》 259 (5091): 94–7. Bibcode:1993Sci...259...94T. doi:10.1126/science.8418502. PMID8418502.
Cartier N, Hacein-Bey-Abina S, Bartholomae CC, Veres G, Schmidt M, Kutschera I, 외. (November 2009). “Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy”. 《Science》 326 (5954): 818–23. Bibcode:2009Sci...326..818C. doi:10.1126/science.1171242. PMID19892975.
Committee on Human Gene Editing: Scientific, Medical, and Ethical Considerations. “Human Genome Editing: Science, Ethics, and Governance”. 《nationalacademies.org》. National Academy of Sciences; National Academy of Medicine. 2017년 2월 21일에 확인함. CS1 관리 - 여러 이름 (링크)
Bainbridge JW, Smith AJ, Barker SS, Robbie S, Henderson R, Balaggan K, 외. (May 2008). “Effect of gene therapy on visual function in Leber's congenital amaurosis”. 《The New England Journal of Medicine》 358 (21): 2231–9. doi:10.1056/NEJMoa0802268. PMID18441371.
Fischer A, Hacein-Bey-Abina S, Cavazzana-Calvo M (June 2010). “20 years of gene therapy for SCID”. 《Nature Immunology》 11 (6): 457–60. doi:10.1038/ni0610-457. PMID20485269.
Ferrua F, Brigida I, Aiuti A (December 2010). “Update on gene therapy for adenosine deaminase-deficient severe combined immunodeficiency”. 《Current Opinion in Allergy and Clinical Immunology》 10 (6): 551–6. doi:10.1097/ACI.0b013e32833fea85. PMID20966749.
Cartier N, Aubourg P (July 2010). “Hematopoietic stem cell transplantation and hematopoietic stem cell gene therapy in X-linked adrenoleukodystrophy”. 《Brain Pathology》 20 (4): 857–62. doi:10.1111/j.1750-3639.2010.00394.x. PMID20626747.
LeWitt PA, Rezai AR, Leehey MA, Ojemann SG, Flaherty AW, Eskandar EN, 외. (April 2011). “AAV2-GAD gene therapy for advanced Parkinson's disease: a double-blind, sham-surgery controlled, randomised trial”. 《The Lancet. Neurology》 10 (4): 309–19. doi:10.1016/S1474-4422(11)70039-4. PMID21419704.
Pearson S, Jia H, Kandachi K (January 2004). “China approves first gene therapy”. 《Nature Biotechnology》 22 (1): 3–4. doi:10.1038/nbt0104-3. PMID14704685.
Pezzoli D, Chiesa R, De Nardo L, Candiani G (September 2012). “We still have a long way to go to effectively deliver genes!”. 《Journal of Applied Biomaterials & Functional Materials》 10 (2): 82–91. doi:10.5301/JABFM.2012.9707. PMID23015375.
Cepko CL, Roberts BE, Mulligan RC (July 1984). “Construction and applications of a highly transmissible murine retrovirus shuttle vector”. 《Cell》 37 (3): 1053–62. doi:10.1016/0092-8674(84)90440-9. PMID6331674.
Blaese RM, Culver KW, Miller AD, Carter CS, Fleisher T, Clerici M, 외. (October 1995). “T lymphocyte-directed gene therapy for ADA- SCID: initial trial results after 4 years”. 《Science》 270 (5235): 475–80. Bibcode:1995Sci...270..475B. doi:10.1126/science.270.5235.475. PMID7570001.
Trojan J, Johnson TR, Rudin SD, Ilan J, Tykocinski ML, Ilan J (January 1993). “Treatment and prevention of rat glioblastoma by immunogenic C6 cells expressing antisense insulin-like growth factor I RNA”. 《Science》 259 (5091): 94–7. Bibcode:1993Sci...259...94T. doi:10.1126/science.8418502. PMID8418502.
Cartier N, Hacein-Bey-Abina S, Bartholomae CC, Veres G, Schmidt M, Kutschera I, 외. (November 2009). “Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy”. 《Science》 326 (5954): 818–23. Bibcode:2009Sci...326..818C. doi:10.1126/science.1171242. PMID19892975.
Yang ZJ, Zhang YR, Chen B, Zhang SL, Jia EZ, Wang LS, 외. (July 2009). “Phase I clinical trial on intracoronary administration of Ad-hHGF treating severe coronary artery disease”. 《Molecular Biology Reports》 36 (6): 1323–9. doi:10.1007/s11033-008-9315-3. PMID18649012.
Hahn W, Pyun WB, Kim DS, Yoo WS, Lee SD, Won JH, 외. (October 2011). “Enhanced cardioprotective effects by coexpression of two isoforms of hepatocyte growth factor from naked plasmid DNA in a rat ischemic heart disease model”. 《The Journal of Gene Medicine》 13 (10): 549–55. doi:10.1002/jgm.1603. PMID21898720.
Deev RV, Bozo IY, Mzhavanadze ND, Voronov DA, Gavrilenko AV, Chervyakov YV, 외. (September 2015). “pCMV-vegf165 Intramuscular Gene Transfer is an Effective Method of Treatment for Patients With Chronic Lower Limb Ischemia”. 《Journal of Cardiovascular Pharmacology and Therapeutics》 20 (5): 473–82. doi:10.1177/1074248415574336. PMID25770117.
Fernàndez-Ruiz I (March 2016). “Gene therapy: No improvement in outcomes with gene therapy for heart failure”. 《Nature Reviews. Cardiology》 13 (3): 122–3. doi:10.1038/nrcardio.2016.14. PMID26843287.
Biffi A, Montini E, Lorioli L, Cesani M, Fumagalli F, Plati T, 외. (August 2013). “Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy”. 《Science》 341 (6148): 1233158. doi:10.1126/science.1233158. PMID23845948.
Olowoyeye A, Okwundu CI (November 2016). “Gene therapy for sickle cell disease”. 《The Cochrane Database of Systematic Reviews》 11: CD007652. doi:10.1002/14651858.CD007652.pub5. PMID27841932.
Powell R, Buchanan A (February 2011). “Breaking evolution's chains: the prospect of deliberate genetic modification in humans”. 《The Journal of Medicine and Philosophy》 36 (1): 6–27. doi:10.1093/jmp/jhq057. PMID21228084.
“International Law”. The Genetics and Public Policy Center, Johns Hopkins University Berman Institute of Bioethics. 2010. 2 September 2014에 원본 문서에서 보존된 문서.