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T. Yokota, E. Pistilli, W. Duddy, K. Nagaraju. Potential of oligonucleotide-mediated exon-skipping therapy for Duchenne muscular dystrophy. „Expert Opin Biol Ther”. 7 (6), s. 831–842, czerwiec 2007. DOI: 10.1517/14712598.7.6.831. PMID: 17555369.
J. Chinen, JM. Puck. Successes and risks of gene therapy in primary immunodeficiencies. „J Allergy Clin Immunol”. 113 (4), s. 595–603; quiz 604, kwiecień 2004. DOI: 10.1016/j.jaci.2004.01.765. PMID: 15100660.
R.A. Morgan, M.E. Dudley, J.R. Wunderlich, M.S. Hughes i inni. Cancer regression in patients after transfer of genetically engineered lymphocytes. „Science”. 314 (5796), s. 126–129, październik 2006. DOI: 10.1126/science.1129003. PMID: 16946036.