Enzyme replacement improves nervous system pathology and function in a mouse model for metachromatic leukodystrophy. Hum. Mol. Genet. 14 (9): 1139–52. May 2005. doi:10.1093/hmg/ddi126. PMID15772092.
Enzyme, cell and gene-based therapies for metachromatic leukodystrophy. J. Inherit. Metab. Dis. 30 (2): 175–83. April 2007. doi:10.1007/s10545-007-0540-z. PMID17347913.
Enzyme replacement improves nervous system pathology and function in a mouse model for metachromatic leukodystrophy. Hum. Mol. Genet. 14 (9): 1139–52. May 2005. doi:10.1093/hmg/ddi126. PMID15772092.
Enzyme, cell and gene-based therapies for metachromatic leukodystrophy. J. Inherit. Metab. Dis. 30 (2): 175–83. April 2007. doi:10.1007/s10545-007-0540-z. PMID17347913.