Blaese R. M., Culver K. W., Miller A. D., Carter C. S., Fleisher T., Clerici M., Shearer G., Chang L., Chiang Y., Tolstoshev P., Greenblatt J. J., Rosenberg S. A., Klein H., Berger M., Mullen C. A., Ramsey W. J., Muul L., Morgan R. A., Anderson W. F. T lymphocyte-directed gene therapy for ADA- SCID: initial trial results after 4 years (англ.) // Science : journal. — 1995. — October (vol. 270, no. 5235). — P. 475—480. — doi:10.1126/science.270.5235.475. — Bibcode: 1995Sci...270..475B. — PMID7570001.
András M. Komáromy,John J. Alexander, Jessica S. Rowlan, Monique M. Garcia, Vince A. Chiodo, Asli Kaya, Jacqueline C. Tanaka, Gregory M. Acland, William W. Hauswirth и Gustavo D. Aguirre1. Gene therapy rescues cone function in congenital achromatopsia (англ.) // Human Molecular Genetics[англ.]. — Oxford University Press, 2010. — Vol. 19, iss. 13. — P. 2581—2593. — doi:10.1093/hmg/ddq136.
Gori, J. L., Hsu, P. D., Maeder, M. L., Shen, S., Welstead, G. G., & Bumcrot, D. (2015). Delivery and Specificity of CRISPR/Cas9 Genome Editing Technologies for Human Gene Therapy. Human gene therapy, 26(7), 443—451. doi:10.1089/hum.2015.074
Wu, Y., Zhou, H., Fan, X., Zhang, Y., Zhang, M., Wang, Y., … & Tang, W. (2015). Correction of a genetic disease by CRISPR-Cas9-mediated gene editing in mouse spermatogonial stem cells. Cell research, 25(1), 67-79. doi:10.1038/cr.2014.160
Pellagatti, A., Dolatshad, H., Valletta, S., & Boultwood, J. (2015). Application of CRISPR/Cas9 genome editing to the study and treatment of disease. Archives of toxicology, 1-12. doi:10.1007/s00204-015-1504-y
Aiuti, A.; Biasco, L.; Scaramuzza, S.; Ferrua, F.; Cicalese, M. P.; Baricordi, C.; Dionisio, F.; Calabria, A. et al. (2013). «Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome». Science. doi: 10.1126/science.1233151.
Blaese R. M., Culver K. W., Miller A. D., Carter C. S., Fleisher T., Clerici M., Shearer G., Chang L., Chiang Y., Tolstoshev P., Greenblatt J. J., Rosenberg S. A., Klein H., Berger M., Mullen C. A., Ramsey W. J., Muul L., Morgan R. A., Anderson W. F. T lymphocyte-directed gene therapy for ADA- SCID: initial trial results after 4 years (англ.) // Science : journal. — 1995. — October (vol. 270, no. 5235). — P. 475—480. — doi:10.1126/science.270.5235.475. — Bibcode: 1995Sci...270..475B. — PMID7570001.
Blaese R. M., Culver K. W., Miller A. D., Carter C. S., Fleisher T., Clerici M., Shearer G., Chang L., Chiang Y., Tolstoshev P., Greenblatt J. J., Rosenberg S. A., Klein H., Berger M., Mullen C. A., Ramsey W. J., Muul L., Morgan R. A., Anderson W. F. T lymphocyte-directed gene therapy for ADA- SCID: initial trial results after 4 years (англ.) // Science : journal. — 1995. — October (vol. 270, no. 5235). — P. 475—480. — doi:10.1126/science.270.5235.475. — Bibcode: 1995Sci...270..475B. — PMID7570001.
[1]Архивная копия от 3 апреля 2018 на Wayback Machine Telomerase gene therapy in adult and old mice d… [EMBO Mol Med. 2012] — PubMed — NCBI
András M. Komáromy,John J. Alexander, Jessica S. Rowlan, Monique M. Garcia, Vince A. Chiodo, Asli Kaya, Jacqueline C. Tanaka, Gregory M. Acland, William W. Hauswirth и Gustavo D. Aguirre1. Gene therapy rescues cone function in congenital achromatopsia (англ.) // Human Molecular Genetics[англ.]. — Oxford University Press, 2010. — Vol. 19, iss. 13. — P. 2581—2593. — doi:10.1093/hmg/ddq136.
